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Kliniska prövningar sponsrade av Office of Rare Diseases (ORD)
Totalt 457 resultat
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... och andra samarbetspartnersAvslutadAndersen-Tawils syndromFörenta staterna
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National Center for Research Resources (NCRR)Ohio State UniversityAvslutadPolyradikuloneuropati, kronisk inflammatorisk demyeliniserande
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National Institute on Drug Abuse (NIDA)Johns Hopkins UniversityOkänd
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National Center for Research Resources (NCRR)Children's Hospital ColoradoOkändLevercirros | Cirros
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National Center for Research Resources (NCRR)Johns Hopkins UniversityAvslutadAminosyrametabolism, medfödda fel
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National Center for Research Resources (NCRR)Ohio State UniversityAvslutadAmyotrofisk lateral skleros | Spinal muskelatrofi | Spinobulbar muskelatrofi
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National Center for Research Resources (NCRR)Virginia Commonwealth UniversityAvslutadSystemisk lupus erythematosus
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National Institute of Diabetes and Digestive and...University of PittsburghAvslutadVulva sjukdomar | Interstitiell cystit
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National Institute of Allergy and Infectious Diseases...University of Alabama at BirminghamAvslutad
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Emory UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Office...IndragenKrampaktig dysfoni | Laryngeal dystoniFörenta staterna
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National Center for Research Resources (NCRR)Baylor College of MedicineAvslutad
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National Center for Research Resources (NCRR)Baylor College of MedicineAvslutad
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National Institute of Neurological Disorders and...Mayo ClinicOkändAkut disseminerad encefalomyelit | Devics syndrom | Marburgs variant av multipel skleros | Balos koncentriska skleros | Akut transversell myelit
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National Center for Research Resources (NCRR)Children's Hospital of PhiladelphiaAvslutadOsteoporos | Osteopeni | Major talassemi
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of...AvslutadJättecellarterit | Takayasus arteritFörenta staterna, Kanada
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National Institute of Neurological Disorders and...Yale UniversityAvslutad
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National Institute of Dental and Craniofacial Research...Columbia UniversityAvslutadHIV-infektioner | Candidiasis, oral
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National Center for Research Resources (NCRR)University of North CarolinaAvslutadCystisk fibros | Atypical Mycobacterium Infection
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National Institute of Neurological Disorders and...Mayo ClinicAvslutad
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National Center for Research Resources (NCRR)Baylor College of MedicineAvslutad
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National Center for Research Resources (NCRR)University of North CarolinaAvslutad
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National Center for Research Resources (NCRR)Baylor College of MedicineAvslutad
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National Center for Research Resources (NCRR)University of North CarolinaAvslutadHemofili B | Faktor IX-brist
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National Center for Research Resources (NCRR)University of North CarolinaAvslutadVon Willebrands sjukdom
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National Institute of Neurological Disorders and...University of PittsburghOkänd
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National Center for Research Resources (NCRR)Vanderbilt University Medical CenterAvslutadBakteriella infektioner | Cystisk fibros
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National Institute of Allergy and Infectious Diseases...Harvard School of Public Health (HSPH)Avslutad
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases... och andra samarbetspartnersAvslutadTakayasu arteritFörenta staterna, Kanada
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University of CincinnatiNational Center for Research Resources (NCRR); Office of Rare Diseases... och andra samarbetspartnersAvslutadLymfangioleiomyomatosFörenta staterna, Kanada, Japan
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National Center for Research Resources (NCRR)University of California, Los AngelesAvslutad
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National Institute of Neurological Disorders and...Massachusetts General HospitalOkändAmyotrofisk lateral skleros
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National Center for Research Resources (NCRR)University of California, San DiegoAvslutadFanconis syndrom | Cystinos
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National Center for Research Resources (NCRR)University of California, Los AngelesAvslutadPulmonell hypertoni | Respiratory Distress Syndrome | Bronkopulmonell dysplasi
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National Center for Research Resources (NCRR)University of California, San DiegoAvslutad
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National Center for Research Resources (NCRR)Indiana University School of MedicineAvslutad
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National Center for Research Resources (NCRR)University of California, San DiegoAvslutad
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National Institute of Neurological Disorders and...Seattle Children's HospitalOkänd
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National Center for Research Resources (NCRR)University of California, Los AngelesAvslutadPseudohypoparatyreos
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National Center for Research Resources (NCRR)Tulane University School of MedicineAvslutad
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National Center for Research Resources (NCRR)University of California, San DiegoAvslutadHomocystinuri
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National Center for Research Resources (NCRR)University of California, Los AngelesAvslutad
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Avslutad
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)AvslutadCytomegalovirusinfektioner
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Avslutad
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Avslutad
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National Institute of Neurological Disorders and...University of Colorado, DenverOkänd
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National Institute of Neurological Disorders and...Baylor College of MedicineAvslutadPrader-Willis syndrom | DiGeorges syndrom | Williams syndrom | Angelmans syndrom | Smith-Magenis syndrom | Kromosomavvikelser | Shprintzens syndromFörenta staterna
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... och andra samarbetspartnersAvslutadHjärnsjukdomar, metabola, medfödda | Ornitin-transkarbamylasbrist | UreacykelstörningFörenta staterna
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National Center for Research Resources (NCRR)Oregon Health and Science UniversityAvslutadBrådmogen pubertet
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer CenterAvslutadMetabolism, medfödda fel | Metionin-adenosyltransferasbrist