搜索临床试验以:Lysosomale Speicherstörungen
总计923个结果
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi Company未知
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Massachusetts General HospitalAlexion Pharmaceuticals未知
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institute... 和其他合作者未知
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National MPS SocietyMediResource Inc.终止
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Eunice Kennedy Shriver National Institute of Child...Washington University School of Medicine; University of Oxford; National Human Genome Research...完全的
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University Hospital, Bordeaux完全的
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Johannes Gutenberg University Mainz未知
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland Medical Center撤销
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Patricia I. Dickson, M.D.The Ryan Foundation终止
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development; The Ryan Foundation终止
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Brigham and Women's HospitalGenzyme, a Sanofi Company未知
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University of Sao PauloFundação de Amparo à Pesquisa do Estado de São Paulo完全的肾病 | 胱氨酸增多症
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University of Rostock完全的
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Klinikum Wels-GrieskirchenGenzyme, a Sanofi Company完全的
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The Hospital for Sick Children完全的
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Nantes University Hospital完全的Patients With Gaucher's Disease法国
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Francisco Marín OrtuñoHospital General Universitario Elche; Hospital Universitario San Juan de Alicante未知右心室肥大 | 法布里病,心脏变异
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Medical University of ViennaMedical University of Graz未知
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BioMarin Pharmaceutical完全的
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The Cooper Health System完全的
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Assistance Publique - Hôpitaux de ParisShire; Zymenex A/S; European Leukodystrophy Association完全的
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Centre Hospitalier Universitaire de Nice完全的
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Clínica de Hidroterapia e Recuperacao FuncionalIntegrated Faculty of Recife终止莫基奥氏病
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Children's National Research InstituteActelion完全的
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National Institute of Arthritis and Musculoskeletal...完全的
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National Institute of Neurological Disorders and...完全的