搜索临床试验以:cystathionine beta synthase deficiency
总计18157个结果
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Leonard S. Marks, M.D.Watson Pharmaceuticals; Solvay Pharmaceuticals完全的
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University of Colorado, DenverEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); University... 和其他合作者完全的
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Federal Research Institute of Pediatric Hematology...完全的
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn School of Medicine... 和其他合作者完全的
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI)终止
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Newcastle UniversityPenn State University; International Food Policy Research Institute未知
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Shahid Beheshti University of Medical Sciences未知
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI)完全的
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI)完全的先前治疗过的骨髓增生异常综合征 | 范可尼贫血 | 新生骨髓增生异常综合征 | 缓解期急性髓性白血病美国, 巴西
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Emory University完全的镰状细胞性贫血症 | 范可尼贫血 | 赫勒综合症 | 慢性肉芽肿病 | 严重的先天性中性粒细胞减少症 | 噬血细胞性淋巴组织细胞增生症 | Wiskott-Aldrich 综合症 | Diamond-Blackfan 贫血 | 重度再生障碍性贫血 | 格兰兹曼血小板无力症 | Shwachman-Diamond 综合症 | 重型地中海贫血 | 白细胞粘附缺陷 | 先天性角化不良 | Chediak-Higashi综合征美国
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National Human Genome Research Institute (NHGRI)终止瓜氨酸血症 | 精氨基琥珀酸尿症 | 高精氨酸血症 | 鸟氨酸氨基甲酰转移酶缺乏症 | 氨基甲酰磷酸合酶 I 缺乏症 | N-乙酰谷氨酸合酶缺乏症美国
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Diurnal LimitedSheffield Teaching Hospitals NHS Foundation Trust; Manchester University NHS Foundation Trust; Covanc... 和其他合作者完全的
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World BankDepartment for International Development, United Kingdom; Wits Reproductive Health and HIV Institute 和其他合作者完全的
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UConn HealthEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)完全的
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CANDLE-KIT Trial Study GroupChugai Pharmaceutical; Roche Diagnostics; The Japan Kidney Foundation; Japanese Society for the...终止肾功能不全,慢性 | 贫血 | 维生素 D 缺乏症 | 肾移植日本
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Federal Research Institute of Pediatric Hematology...未知造血干细胞移植 | Wiskott-Aldrich 综合症 | 移植失败俄罗斯联邦
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University of LausanneUniversity of Modena and Reggio Emilia完全的
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University of WashingtonEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Fogarty...完全的
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Grifols Therapeutics LLC终止
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Montefiore Medical CenterNational Institute of Mental Health (NIMH); Albert Einstein College of Medicine; National Institutes...终止
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University of Washington完全的
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Clinical Nutrition Research Centre, Singapore未知
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Fundacion para la Formacion e Investigacion Sanitarias...Germans Trias i Pujol Hospital; Hospital Universitario Virgen de la Arrixaca完全的
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Massachusetts General HospitalUniversity of British Columbia; Dana-Farber Cancer Institute; University of California, San Francisco 和其他合作者完全的
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Novartis Pharmaceuticals完全的骨髓增生异常综合征 | 范可尼综合症 | 贫血,再生障碍性 | Β-地中海贫血 | 贫血,Diamond-Blackfan美国
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Johns Hopkins Bloomberg School of Public HealthUniversity of California, Davis; Newcastle University; HarvestPlus完全的
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University of California, DavisInternational Centre for Diarrhoeal Disease Research, Bangladesh完全的维生素 A 缺乏症
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Boston UniversityBeijing Ditan Hospital; Second People's Hospital, Dali完全的
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Genzyme, a Sanofi Company完全的戈谢病,1 型 | 脑苷脂沉积综合征 | 葡萄糖脑苷脂酶缺乏症 | 葡萄糖神经酰胺β-葡萄糖苷酶缺乏症 | 戈谢病,非神经病形式美国, 以色列, 墨西哥, 俄罗斯联邦, 阿根廷, 意大利