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Kliniske studier sponset av Myhre Syndrome Foundation
Totalt 29 resultater
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Baylor College of MedicineAicardi Syndrome FoundationRekrutteringHjernesykdommer | Aicardis syndromForente stater
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Boston Children's HospitalPhelan-McDermid Syndrome FoundationFullførtIntellektuell funksjonshemming | Autismespektrumforstyrrelse | Phelan-McDermid syndromForente stater
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Boston Children's HospitalInternational Rett Syndrome FoundationFullført
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... og andre samarbeidspartnereRekruttering
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Johns Hopkins UniversityCornelia de Lange Syndrome FoundationHar ikke rekruttert ennåCornelia de Langes syndromForente stater
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University Hospital, BordeauxFondation Syndrome de Rubinstein-TaybiFullførtRubinstein-Taybi syndromFrankrike
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationFullført
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgFullført
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Foundation for Prader-Willi ResearchPrader-Willi Syndrome Association USA; Foundation for Prader-Willi Research... og andre samarbeidspartnereFullførtPrader-Willi syndromForente stater
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Foundation for Angelman Syndrome Therapeutics,...Queensland University of TechnologyRekruttering
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Foundation for Prader-Willi ResearchPrader-Willi Syndrome Association USAFullført
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University of MiamiSjogrens Syndrome Foundation; Microbiome Health Research InstituteFullført
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins... og andre samarbeidspartnereRekrutteringMitokondrielle sykdommer | Retinitis Pigmentosa | Myasthenia Gravis | Eosinofil gastroenteritt | Multippel systematrofi | Leiomyosarkom | Leukodystrofi | Anal fistel | Spinocerebellar ataksi type 3 | Friedreich Ataxia | Kennedy sykdom | Lyme sykdom | Hemofagocytisk lymfohistiocytose | Spinocerebellar ataksi type 1 | Spinocerebellar... og andre forholdForente stater, Australia
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University of ArkansasDown Syndrome Research Foundation; Arkansas Children Research InstituteTilbaketrukketDowns syndrom
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationFullført
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William Ondo, MDRestless Legs Syndrome FoundationUkjentRestless Legs Syndrome | ForstørrelseForente stater
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Washington University School of MedicineShwachman Diamond Syndrome Foundation; Barnes-Jewish HospitalRekruttering
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University of OxfordHoffmann-La Roche; Foundation for Angelman Syndrome Therapeutics UKRekruttering
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University of Colorado, DenverNational Center for Advancing Translational Sciences (NCATS); Linda Crnic... og andre samarbeidspartnereRekruttering
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University of BernUniversity of Southampton; Selbsthilfegruppe Kartagener Syndrom und Primäre... og andre samarbeidspartnereRekruttering
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University of Kansas Medical CenterHarvard Medical School (HMS and HSDM); Foundation for Prader-Willi Research og andre samarbeidspartnereFullførtHyperfagi | Prader-Willi syndromForente stater
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); American Thoracic Society og andre samarbeidspartnereFullførtAkutt lungesviktsyndrom | Akutt lungeskade | Respiratorisk distress syndrom, voksenForente stater, Canada
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbeidspartnereRekruttering
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Wen-Hann TanBaylor College of Medicine; University of California, San Francisco; Vanderbilt... og andre samarbeidspartnereFullført
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbeidspartnereFullførtRett syndrom, bevart talevariant | Mecp2 dupliseringssyndrom | Rett-relaterte lidelserForente stater
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Massachusetts General HospitalMayo Clinic; University of Pennsylvania; University of South Florida; University... og andre samarbeidspartnereFullført
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbeidspartnereRekrutteringIntellektuell funksjonshemming | Autismespektrumforstyrrelse | Phelan-McDermid syndromForente stater
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University... og andre samarbeidspartnereRekrutteringSykdommer i nervesystemet | Nevrologiske manifestasjoner | Nevroatferdsmanifestasjoner | Genetiske sykdommer, X-linked | Intellektuell funksjonshemming | Nevroutviklingsforstyrrelser | Nevrologisk lidelse | Rett syndrom | Genetisk sykdom | Rett syndrom, atypiskForente stater