重型阿尔法地中海贫血的临床试验
总计3379个结果
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Permian Health Lung InstituteThe Gambia Committee on Traditional Practices Affecting the Health of Women and Children (GAMCOTRAP)尚未招聘
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Isfahan University of Medical SciencesMadaus Inc未知
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Editas Medicine, Inc.招聘中
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Novartis; University... 和其他合作者终止
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Cure CMD招聘中Emery-Dreifuss 肌营养不良症 | 先天性肌无力综合症 | 肢带型肌营养不良症 | ITGA7(整合素 Alpha-7)缺乏症导致的先天性肌营养不良症 | Α-Dystroglycanopathy(先天性肌肉萎缩症和 Dystroglycan 异常糖基化伴有严重癫痫) | Α-肌营养不良症(由 TRAPPC11 突变引起的先天性肌营养不良伴脂肪肝和婴儿期白内障) | Α-Dystroglycanopathy(先天性肌营养不良症伴 Dystroglycan 低糖基化) | Α-肌营养不良症(先天性肌营养不良伴肌营养不良和癫痫) | Alpha-Dystroglycanopathy(Dystroglycanopathy... 及其他条件美国
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Laboratoire français de Fractionnement et de Biotechnologies完全的Α 1-抗胰蛋白酶缺乏症
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University of FloridaAlpha-1 Foundation; Brantly, Mark L., M.D.完全的
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Affiliated hospital of guangxi medical university...Zhongshan Hospital Xiamen University; The Affiliated Nanjing Drum Tower Hospital of Nanjing... 和其他合作者未知
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Celgene终止
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Children's Hospital of PhiladelphiaAnn & Robert H Lurie Children's Hospital of Chicago; The Cooley's Anemia Foundation,完全的
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IRCCS San RaffaeleTelethon Institute for Gene Therapy (OSR-TIGET)主动,不招人
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Wave Life Sciences Ltd.尚未招聘Alpha-1 抗胰蛋白酶缺乏症
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Wave Life Sciences Ltd.招聘中
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Kamada, Ltd.Syneos Health招聘中
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Baxalta now part of Shire完全的
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)完全的
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National Jewish HealthMedical University of South Carolina未知
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Medical University of South CarolinaNational Center for Research Resources (NCRR); Alpha-1 Foundation完全的
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Grifols Therapeutics LLC完全的
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Grifols Therapeutics LLC完全的
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National Center for Research Resources (NCRR)University of Pittsburgh终止
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Rambam Health Care CampusHadassah Medical Organization; Tel-Aviv Sourasky Medical Center; Soroka University Medical Center完全的
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Institute of Hematology & Blood Diseases Hospital...Shanghai Vitalgen BioPharma Co., Ltd.招聘中
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UCSF Benioff Children's Hospital OaklandNovartis Pharmaceuticals完全的
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Hospital Universitari Vall d'Hebron Research InstituteEuropean Respiratory Society招聘中
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk company主动,不招人Α 1-抗胰蛋白酶缺乏症英国, 美国, 爱尔兰, 比利时, 新西兰, 西班牙, 荷兰, 葡萄牙, 加拿大, 澳大利亚, 法国, 奥地利, 德国, 瑞典
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St. Louis UniversityBoston University; University College, London; University of Massachusetts, Worcester; University... 和其他合作者主动,不招人
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Arrowhead Pharmaceuticals终止
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Kamada, Ltd.完全的
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)完全的
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Beam Therapeutics Inc.尚未招聘
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Vertex Pharmaceuticals Incorporated主动,不招人
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Arrowhead Pharmaceuticals完全的
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Fondazione Salvatore MaugeriAzienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia; Grifols Biologicals, LLC; IRCCS Policlinico S. Matteo完全的Alpha-1 抗胰蛋白酶缺乏症
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Arrowhead Pharmaceuticals撤销
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National Center for... 和其他合作者完全的