X-koblet kreatinmangel的临床试验
总计1835个结果
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institute... 和其他合作者未知
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University Health Network, TorontoUniversity of Colorado, Denver; Mayo Clinic; Icahn School of Medicine at Mount Sinai; Alberta Health... 和其他合作者招聘中
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The University of Queensland招聘中
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Canadian Fabry Research ConsortiumNova Scotia Health Authority招聘中
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University Hospital Erlangen完全的
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Ospedale San DonatoAmicus Therapeutics; Institute of Biomedicine and Molecular Immunology - CNR完全的
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study site完全的贝克尔肌营养不良症 | 肢带型肌营养不良症,2A 型(钙蛋白酶 3 缺乏症) | 肢带型肌营养不良症,2B 型(Miyoshi 肌病,Dysferlin 缺乏症) | 肢带型肌营养不良症,2I 型(FKRP 缺乏症)美国
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Mirum Pharmaceuticals, Inc.Children's Hospital Medical Center, Cincinnati完全的
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Westfälische Wilhelms-Universität MünsterChiesi GmbH招聘中
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Hospital Clinico Universitario de SantiagoAlvaro Hermida (Co-IP); Susana Belen Bravo; Maria Teresa Cardoso; Cristobal Colon Mejeras; Maria Jose... 和其他合作者招聘中
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University Health Network, TorontoOzmosis Research Inc.完全的
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ProtalixChiesi Farmaceutici S.p.A.完全的法布里病美国, 丹麦, 比利时, 英国, 挪威, 意大利, 捷克语
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Chiesi Farmaceutici S.p.A.Iqvia Pty Ltd; Protalix完全的
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation Trust完全的
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Children's Hospital of Fudan UniversityFirst Affiliated Hospital, Sun Yat-Sen University; Wuhan Union Hospital, China; Beijing Children... 和其他合作者撤销
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.完全的
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Amicus Therapeutics终止