代谢性先天性脑病的临床试验
总计87528个结果
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)完全的
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BioMarin Pharmaceutical完全的
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Genzyme, a Sanofi Company完全的
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Amicus Therapeutics主动,不招人
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)完全的
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National Taiwan University Hospital未知
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Genzyme, a Sanofi Company完全的
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi Company未知
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BioMarin Pharmaceutical完全的苯丙酮尿症 (PKU) 或四氢生物蝶呤 (BH4) 缺乏症导致的高苯丙氨酸血症 (HPA)瑞典, 法国, 意大利, 西班牙, 德国, 荷兰, 奥地利, 斯洛伐克, 葡萄牙
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Lysosomal and Rare Disorders Research and Treatment...招聘中
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IntraBio Inc完全的
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, Worcester主动,不招人
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National Institute of Neurological Disorders and...完全的
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Travere Therapeutics, Inc.招聘中
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Hospital de Clinicas de Porto AlegreFundação de Amparo à Pesquisa do Estado do Rio Grande do Sul, Brazil暂停
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Andrea GropmanChildren's National Research Institute完全的
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Ultragenyx Pharmaceutical Inc主动,不招人
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Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical Sciences招聘中
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The Hospital for Sick ChildrenActelion完全的