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Søg i kliniske forsøg efter: Lysomale Speicherkrankheit
I alt 945 resultater
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Francisco Marín OrtuñoHospital General Universitario Elche; Hospital Universitario San Juan de...UkendtHøjre ventrikulær hypertrofi | Fabrys sygdom, hjertevariant
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National Institute of Neurological Disorders and...AfsluttetFabrys sygdomForenede Stater
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Rambam Health Care CampusUkendt
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Medical University of ViennaMedical University of GrazUkendtFabrys sygdom | Venstre ventrikulær hypertrofiØstrig
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VI | Maroteaux-Lamy syndromForenede Stater, Portugal, Frankrig
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Centre Hospitalier Universitaire de NiceUkendt
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The Cooper Health SystemAfsluttetMetakromatisk leukodystrofiForenede Stater
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Assistance Publique - Hôpitaux de ParisShire; Zymenex A/S; European Leukodystrophy AssociationAfsluttetMetakromatisk leukodystrofiFrankrig
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Centre Hospitalier Universitaire de NiceAfsluttet
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Amicus TherapeuticsAfsluttetGauchers sygdomForenede Stater
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Amicus TherapeuticsAfsluttetType 1 Gauchers sygdomForenede Stater, Det Forenede Kongerige
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ActelionAfsluttet
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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Clínica de Hidroterapia e Recuperacao FuncionalIntegrated Faculty of RecifeAfsluttetMorquios sygdom
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Amicus TherapeuticsAfsluttetGlykogenopbevaringssygdom type II | Pompes sygdomForenede Stater
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Children's National Research InstituteActelionAfsluttetSandhoffs sygdom | GM2 Gangliosidoser | Tay-SachsForenede Stater
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National Institute of Arthritis and Musculoskeletal...AfsluttetMyositis | Dermatomyositis | Polymyositis | Glykogenopbevaringssygdom type II | Glykogen Opbevaring Sygdom Type VIIForenede Stater
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National Institute of Neurological Disorders and...AfsluttetNeoplasma i hjernen | Alzheimers sygdom | Niemann Pick sygdomForenede Stater
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National Institute of Neurological Disorders and...AfsluttetFabrys sygdomForenede Stater
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National Institute of Neurological Disorders and...Afsluttet
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National Institute of Neurological Disorders and...AfsluttetSund og rask | Motor neuron sygdom | Lysosomal opbevaringssygdom | Bevægelsesforstyrrelse | Demyeliniserende sygdomForenede Stater
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National Institute of Neurological Disorders and...AfsluttetSund og rask | Fabrys sygdom | Cerebrovaskulær ulykkeForenede Stater
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National Institute of Neurological Disorders and...Afsluttet
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National Institute of Mental Health (NIMH)Afsluttet
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National Eye Institute (NEI)AfsluttetCystinoseForenede Stater
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National Institute of Neurological Disorders and...AfsluttetFabrys sygdomForenede Stater
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National Institute of Neurological Disorders and...AfsluttetGauchers sygdomForenede Stater
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National Institute of Neurological Disorders and...Afsluttet
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Eunice Kennedy Shriver National Institute of Child...AfsluttetGlykogenopbevaringssygdomForenede Stater
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National Institute of Neurological Disorders and...AfsluttetSund og rask | Fabrys sygdomForenede Stater
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Assistance Publique - Hôpitaux de ParisUkendt
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ProtalixAfsluttet
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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National Center for Research Resources (NCRR)University of MichiganAfsluttet
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National Center for Research Resources (NCRR)University of PittsburghUkendtGauchers sygdomForenede Stater
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National Center for Research Resources (NCRR)University of California, Los AngelesAfsluttetTrombocytopeni | Medfødte metabolismefejl | Metakromatisk leukodystrofi | Fanconis anæmi | Major Thalassæmi | Ren rødcellet aplasiForenede Stater
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaAfsluttet
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National Center for Research Resources (NCRR)Eunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetCystinoseForenede Stater
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Fairview University Medical CenterUkendtMucopolysaccharidosis I | Niemann-Pick sygdom | Mucopolysaccharidosis VI | Wolmans sygdom | Adrenoleukodystrofi | Metakromatisk leukodystrofi | Lungekomplikationer | Fucosidosis | Globoidcelleleukodystrofi | Gauchers sygdom | Mannosidose | I CellesygdomForenede Stater
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National Center for Research Resources (NCRR)University of California, San DiegoAfsluttetFanconi syndrom | Cystinose
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiAfsluttetMetabolisme, medfødte fejl | Leukodystrofi, globoidcelle | Tay-Sachs sygdom | Porfyri, erytropoietiskForenede Stater
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National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttet