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Kliniske studier sponset av Office of Rare Diseases (ORD)
Totalt 457 resultater
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... og andre samarbeidspartnereAvsluttetAndersen-Tawil syndromForente stater
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National Center for Research Resources (NCRR)Ohio State UniversityFullførtPolyradiculonevropati, kronisk inflammatorisk demyeliniserende
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National Institute on Drug Abuse (NIDA)Johns Hopkins UniversityUkjent
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National Center for Research Resources (NCRR)Children's Hospital ColoradoUkjentLevercirrhose | Skrumplever
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National Center for Research Resources (NCRR)Johns Hopkins UniversityFullførtAminosyremetabolisme, medfødte feil
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National Center for Research Resources (NCRR)Ohio State UniversityFullførtAmyotrofisk lateral sklerose | Spinal muskelatrofi | Spinobulbar muskelatrofi
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National Center for Research Resources (NCRR)Virginia Commonwealth UniversityFullførtSystemisk lupus erythematosus
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National Institute of Diabetes and Digestive and...University of PittsburghFullførtVulva sykdommer | Interstitiell blærebetennelse
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Emory UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Office...TilbaketrukketSpasmodisk dysfoni | Laryngeal dystoniForente stater
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National Center for Research Resources (NCRR)Baylor College of MedicineFullført
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National Center for Research Resources (NCRR)Baylor College of MedicineFullført
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National Institute of Neurological Disorders and...Mayo ClinicUkjentAkutt disseminert encefalomyelitt | Devics syndrom | Marburgs variant av multippel sklerose | Balos konsentriske sklerose | Akutt tverrmyelitt
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National Center for Research Resources (NCRR)Children's Hospital of PhiladelphiaFullførtOsteoporose | Osteopeni | Major Thalassemia
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National Institute of Allergy and Infectious Diseases...University of Alabama at BirminghamFullført
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National Institute of Neurological Disorders and...Yale UniversityFullført
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National Institute of Dental and Craniofacial Research...Columbia UniversityFullførtHIV-infeksjoner | Candidiasis, oral
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National Center for Research Resources (NCRR)University of North CarolinaFullførtCystisk fibrose | Atypical Mycobacterium Infection
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of...FullførtKjempecellearteritt | Takayasus arterittForente stater, Canada
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National Institute of Neurological Disorders and...Mayo ClinicFullført
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National Center for Research Resources (NCRR)Baylor College of MedicineFullført
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National Center for Research Resources (NCRR)University of North CarolinaFullført
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National Center for Research Resources (NCRR)Baylor College of MedicineFullført
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National Center for Research Resources (NCRR)University of North CarolinaFullførtHemofili B | Faktor IX-mangel
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National Center for Research Resources (NCRR)University of North CarolinaFullførtVon Willebrands sykdom
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National Institute of Neurological Disorders and...University of PittsburghUkjent
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National Center for Research Resources (NCRR)Vanderbilt University Medical CenterFullførtBakterielle infeksjoner | Cystisk fibrose
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National Institute of Allergy and Infectious Diseases...Harvard School of Public Health (HSPH)Fullført
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbeidspartnereFullførtTakayasu arterittForente stater, Canada
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University of CincinnatiNational Center for Research Resources (NCRR); Office of Rare Diseases... og andre samarbeidspartnereFullførtLymfangioleiomyomatoseForente stater, Canada, Japan
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National Center for Research Resources (NCRR)University of California, Los AngelesFullført
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National Institute of Neurological Disorders and...Massachusetts General HospitalUkjentAmyotrofisk lateral sklerose
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National Center for Research Resources (NCRR)University of California, San DiegoFullførtFanconi syndrom | Cystinose
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National Center for Research Resources (NCRR)University of California, Los AngelesFullførtPulmonal hypertensjon | Respiratorisk distress syndrom | Bronkopulmonal dysplasi
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National Center for Research Resources (NCRR)University of California, San DiegoFullført
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National Center for Research Resources (NCRR)Indiana University School of MedicineFullført
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National Center for Research Resources (NCRR)University of California, San DiegoFullført
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National Institute of Neurological Disorders and...Seattle Children's HospitalUkjent
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National Center for Research Resources (NCRR)University of California, Los AngelesFullførtPseudohypoparathyroidisme
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National Center for Research Resources (NCRR)Tulane University School of MedicineFullført
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National Center for Research Resources (NCRR)University of California, San DiegoFullførtHomocystinuri
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National Center for Research Resources (NCRR)University of California, Los AngelesFullført
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Fullført
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)FullførtCytomegalovirusinfeksjoner
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Fullført
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Fullført
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National Institute of Neurological Disorders and...University of Colorado, DenverUkjent
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... og andre samarbeidspartnereFullførtHjernesykdommer, metabolske, medfødte | Ornithine Transcarbamylase mangel | Urea syklus lidelseForente stater
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National Institute of Neurological Disorders and...Baylor College of MedicineFullførtPrader-Willi syndrom | DiGeorge syndrom | Williams syndrom | Angelman syndrom | Smith-Magenis syndrom | Kromosomavvik | Shprintzen syndromForente stater
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National Center for Research Resources (NCRR)Oregon Health and Science UniversityFullførtTidlig pubertet
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer CenterFullførtMetabolisme, medfødte feil | Metionin adenosyltransferase mangel