锥杆营养不良的临床试验
总计17358个结果
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Sarepta Therapeutics, Inc.招聘中
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Newcastle-upon-Tyne Hospitals NHS TrustJain Foundation主动,不招人肌铁蛋白病 | LGMD2B 现在归类为 LGMDR2 | 三好肌病大韩民国, 智利, 西班牙, 美国, 丹麦, 法国, 意大利, 日本, 英国
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Muscular Dystrophy...完全的
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Castle Creek Pharmaceuticals, LLC完全的
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PTC Therapeutics终止
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Charite University, Berlin, Germany完全的开裂型牙槽骨缺损 | 一阶段骨增强
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PYC Therapeutics招聘中
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Innostellar Biotherapeutics Co.,Ltd主动,不招人
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Sarepta Therapeutics, Inc.主动,不招人
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Recep Tayyip Erdogan University Training and Research...完全的
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aTyr Pharma, Inc.完全的
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The Immunobiological Technology Institute (Bio-Manguinhos)...未知肾功能不全,慢性 | 红细胞再生障碍,纯
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Sunnybrook Health Sciences CentrePrincess Margaret Hospital, Canada; Juravinski Cancer Center未知
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)终止
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AstraZeneca终止胃癌 | 晚期实体瘤 | 实体瘤 | Child-Pugh A 至 B7 晚期肝细胞癌 | EGFR 和/或 ROS 突变型 NSCLC | 肺转移癌大韩民国
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI); National Marrow... 和其他合作者招聘中先天性无巨核细胞性血小板减少症 | 阵发性睡眠性血红蛋白尿 | Shwachman-Diamond 综合症 | 骨髓衰竭综合症 | 先天性纯红细胞再生障碍 | 遗传性铁粒幼细胞性贫血 | 伴有种系 GATA2 突变的血液肿瘤 | 具有种系 SAMD9 突变的血液肿瘤 | 具有种系 SAMD9L 突变的血液肿瘤美国
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Oak Hill Bio Ltd终止
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St. Jude Children's Research Hospital完全的
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Seoul National University Hospital撤销
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University Hospital, Basel, SwitzerlandInstitute of Molecular and Clinical Ophthalmology Basel招聘中
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Netherlands Institute for Innovative Ocular SurgeryAmnitrans Eyebank Rotterdam; Melles CorneaClinic Rotterdam完全的
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Cooperative International Neuromuscular Research...United States Department of Defense完全的
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)完全的
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Boston Children's HospitalMuscular Dystrophy Association招聘中
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Phoenicis Therapeutics终止一项双盲、随机、受试者内安慰剂对照、多中心、多剂量研究,评估安全性、机制证明、初步疗效和全身暴露在已确诊 DDEB 或 RDEB 诊断且外显子 73 中有一个或多个致病性突变的受试者中COL7A1基因营养不良大疱性表皮松解症,隐性 | 营养不良性大疱性表皮松解,显性美国, 西班牙, 法国
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Zhongshan Ophthalmic Center, Sun Yat-sen University招聘中
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Netherlands Institute for Innovative Ocular SurgeryAmnitrans Eyebank Rotterdam完全的
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)完全的
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Johnson & Johnson Pharmaceutical Research & Development...完全的红细胞再生障碍,纯 | 慢性肾功能衰竭
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Stanford UniversityUniversity of Alabama at Birmingham; University of Minnesota完全的镰状细胞性贫血症 | 地中海贫血 | Diamond-Blackfan 贫血美国
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Asklepios Biopharmaceutical, Inc.招聘中肌营养不良症 | 肢带型肌营养不良症 | LGMD2I | LGMD | 2 型肢带型肌营养不良症 | LGMD2 | FKRP | FKRP突变 | Fukutin 相关蛋白美国
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico; Istituto Giannina... 和其他合作者邀请报名
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Region Stockholm尚未招聘Systemic Oxygenation vs ROS Formation in TBI Patients瑞典