线粒体遗传病的临床试验
总计151826个结果
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University of South FloridaFriedreich's Ataxia Research Alliance; Edison Pharmaceuticals Inc完全的
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical Inc不再可用巴特综合症 | 线粒体三功能蛋白缺乏症 | 极长链酰基辅酶 A 脱氢酶 (VLCAD) 缺乏症 | 肉碱棕榈酰转移酶缺乏症(CPT1、CPT2) | 长链羟酰辅酶 A 脱氢酶缺乏症 | 糖原贮积障碍 | 丙酮酸羧化酶缺乏症 | 酰基辅酶 A 脱氢酶家族,成员 9,缺乏美国
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Sanquin-LUMC J.J van Rood Center for Clinical Transfusion...Leiden University Medical Center完全的
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Massachusetts General HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)未知
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)招聘中
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases Clinical Research...招聘中
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Byron LamNational Eye Institute (NEI)主动,不招人
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Santhera Pharmaceuticals完全的
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Murdoch Childrens Research InstituteFriedreich's Ataxia Research Alliance完全的
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Nantes University HospitalUniversity Hospital, Angers; University Hospital, Brest; Rennes University Hospital; University...完全的
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Jirair Krikor BedoyanUltragenyx Pharmaceutical Inc招聘中
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Saol... 和其他合作者主动,不招人
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The University of Texas Health Science Center at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)完全的
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of Rochester招聘中
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University of MinnesotaFriedreich's Ataxia Research Alliance; Bob Allison Ataxia Research Center完全的
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Stealth BioTherapeutics Inc.完全的
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Adverum Biotechnologies, Inc.Adverum Biotechnologies SAS, a wholly owned subsidiary of Adverum Biotechnologies, Inc.完全的
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Oregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Oregon State University终止
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Sanquin-LUMC J.J van Rood Center for Clinical Transfusion...Leiden University Medical Center完全的
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Medical University of Graz完全的
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Steen Hvitfeldt Poulsen完全的
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Sanquin-LUMC J.J van Rood Center for Clinical Transfusion...Erasmus Medical Center; Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA); Leiden...终止
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Eunice Kennedy Shriver National Institute of Child...招聘中
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Institut National de la Santé Et de la Recherche...Commissariat A L'energie Atomique; Imagine Institute完全的
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IRCCS San RaffaeleAzienda Socio Sanitaria Territoriale della Valle Olona招聘中