单羧酸转运蛋白 8 缺陷的临床试验
总计179个结果
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Dana-Farber Cancer Institute未知
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Inozyme Pharma尚未招聘婴儿广泛性动脉钙化 | 常染色体隐性低血磷性佝偻病 | 外核苷酸焦磷酸酶/磷酸二酯酶 1 缺乏症 | ATP 结合盒亚家族 C 成员 6 缺陷
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Assistance Publique - Hôpitaux de ParisEuroFancolen完全的
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)完全的
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical Center, Cincinnati完全的
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)完全的
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products Development完全的
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Masonic Cancer Center, University of Minnesota完全的
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERER完全的
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, Cincinnati完全的
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of Texas, Southwestern...终止
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy, Baylor College...终止
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Inozyme Pharma尚未招聘弹性假黄瘤 | 动脉钙化 | 基因突变 | 外核苷酸焦磷酸酶/磷酸二酯酶 1 缺乏症 | 2 型常染色体隐性低血磷性佝偻病
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National Center for Research Resources (NCRR)University of California, San Diego完全的范可尼综合症 | 胱氨酸增多症
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de la Fundación Jiménez... 和其他合作者完全的
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma Limited终止
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)完全的
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NYU Langone HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)完全的
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)完全的未明确的儿童实体瘤,具体方案 | 未明确的成人实体瘤,特定方案 | 范可尼贫血美国
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Universitaire Ziekenhuizen KU LeuvenKU Leuven未知
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institutes... 和其他合作者招聘中
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Westfälische Wilhelms-Universität MünsterICON plc未知
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National Human Genome Research Institute (NHGRI)完全的