丙酮酸代谢,先天性错误的临床试验
总计4350个结果
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PTC Therapeutics招聘中
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Ajinomoto Co., Inc.Great Ormond Street Hospital for Children NHS Foundation Trust; Birmingham Children's Hospital主动,不招人
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PTC Therapeutics完全的
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University of British ColumbiaRare Disease Foundation, Vancouver, Canada; Saudi Arabian Cultural Bureau, Ottawa完全的
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BioMarin Pharmaceutical完全的
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Hamilton Health Sciences CorporationChildren's Hospital of Eastern Ontario; McMaster Children's Hospital; BioMarin Pharmaceutical完全的
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Emory UniversityNational PKU Alliance完全的
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Children's Hospital of Philadelphia完全的
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Children's University Hospital, IrelandUniversity College Dublin; Health Research Board, Ireland; Medical Research Charities Group Ireland完全的
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical Research招聘中
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University of PennsylvaniaUniversity of Amsterdam; University of Cape Town; University of Witwatersrand, South Africa招聘中
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LIB Therapeutics LLC完全的
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Organon and CoBayer完全的高胆固醇血症 | 家族性高胆固醇血症 | 纯合谷甾醇血症
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Regeneron PharmaceuticalsSanofi终止
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Regeneron PharmaceuticalsSanofi完全的
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AstraZeneca完全的纯合子家族性高胆固醇血症 (HoFH)马来西亚, 加拿大, 以色列, 荷兰, 台湾, 比利时, 丹麦
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Merck Sharp & Dohme LLC终止
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Novartis完全的混合性血脂异常 | 杂合子家族性高胆固醇血症瑞士
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Homology Medicines, Inc终止