搜索临床试验以:rAAV2-hRPE65
总计84个结果
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, Worcester完全的
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University of PennsylvaniaNational Eye Institute (NEI)主动,不招人
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NightstaRx Ltd, a Biogen Company邀请报名无脉络膜血症 | X连锁视网膜色素变性美国, 英国, 荷兰, 德国, 法国, 巴西, 加拿大, 丹麦, 芬兰
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of Iowa主动,不招人
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Spark Therapeutics主动,不招人RPE65 突变导致的遗传性视网膜营养不良
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Bin Li未知急性 LHON | 三个月内发作 | 在 3 到 6 个月之间发作 | 在 6 到 12 个月之间发作 | 在 12 至 24 个月之间发作 | 在 24 至 60 个月之间发病 | 60 个月以上发病中国
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum für Tumorerkrankungen完全的
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Huazhong University of Science and TechnologyShiyan Taihe Hospital主动,不招人
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Bin LiHuazhong University of Science and Technology完全的
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University of Oxford; Alberta... 和其他合作者完全的
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UniQure Biopharma B.V.Institut Pasteur; Venn Life Sciences完全的
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital NHS Foundation... 和其他合作者完全的
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National Center for... 和其他合作者完全的
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Jerry R. MendellDuchenne Alliance; Milo Therapeutics完全的
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MeiraGTx, LLC招聘中
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King Khaled Eye Specialist HospitalKing Faisal Specialist Hospital & Research Center完全的
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Nationwide Children's HospitalParent Project Muscular Dystrophy完全的
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University College, LondonMoorfields Eye Hospital NHS Foundation Trust; Targeted Genetics Corporation完全的
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University of FloridaUniversity of Miami; University of Massachusetts, Worcester不再可用
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)完全的
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International AIDS Vaccine InitiativeNational Institute of Allergy and Infectious Diseases (NIAID); Children's Hospital of Philadelphia未知
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Genzyme, a Sanofi Company完全的眼疾 | 黄斑变性 | 视网膜退化 | 基因治疗 | 年龄相关性黄斑病 | 年龄相关性黄斑病 | 视网膜新生血管 | 与年龄相关的黄斑病 | 黄斑病变,年龄相关 | 治疗,基因美国
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National Center for... 和其他合作者完全的
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical Emas完全的
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)完全的
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Muscular Dystrophy...完全的
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Brain Neurotherapy Bio, Inc.California Institute for Regenerative Medicine (CIRM); Asklepios Biopharmaceutical, Inc.主动,不招人