氨基酸代谢,先天性错误的临床试验
总计5634个结果
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University of California, San...招聘中
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Arcturus Therapeutics, Inc.主动,不招人
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham Women's and Children...尚未招聘黑尿症 | 同型半胱氨酸;代谢紊乱 | 酪氨酸血症,I 型 | 酪氨酸血症,II 型 | 酪氨酸血症,III 型 | MSUD(枫糖浆尿病)
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Ultragenyx Pharmaceutical Inc主动,不招人
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Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn School of Medicine... 和其他合作者完全的
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Emma Marie Caroline SlackUniversity Children's Hospital完全的
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Bambino Gesù Hospital and Research InstituteCatholic University of the Sacred Heart完全的
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Baylor College of MedicineChildren's Hospital of Philadelphia; Children's Hospital Colorado; Seattle Children's Hospital; Children...招聘中
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The University of Texas Health Science Center,...BioMarin Pharmaceutical终止
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare... 和其他合作者完全的
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The Hospital for Sick ChildrenBioMarin Pharmaceutical完全的
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research Network; Office...完全的
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Hamilton Health Sciences CorporationChildren's Hospital of Eastern Ontario; McMaster Children's Hospital; BioMarin Pharmaceutical完全的
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Arcturus Therapeutics, Inc.招聘中
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Andrea GropmanChildren's National Research Institute完全的
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iECURE, Inc.招聘中尿素循环障碍,先天性 | 鸟氨酸转氨甲酰酶缺乏症 | 鸟氨酸转氨甲酰酶缺乏症 | 鸟氨酸氨基甲酰转移酶缺乏症(疾病)英国
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Hospital de Clinicas de Porto AlegreFundação de Amparo à Pesquisa do Estado do Rio Grande do Sul, Brazil暂停
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McGill University Health Centre/Research Institute...March of Dimes完全的
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Aeglea Biotherapeutics终止
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Ultragenyx Pharmaceutical Inc招聘中场外交易不足美国, 葡萄牙, 澳大利亚, 意大利, 西班牙, 英国, 日本, 加拿大, 德国, 法国, 阿根廷, 荷兰, 巴西
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Vitaflo International, Ltd招聘中
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Eunice Kennedy Shriver National Institute of Child...Children's National Research Institute终止鸟氨酸转氨甲酰酶缺乏症
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metaX Institut fuer Diatetik GmbHBirmingham Children's Hospital完全的
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, France完全的
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University Hospital, Clermont-Ferrand未知