遗传病,X连锁的临床试验
总计15180个结果
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation Trust完全的
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Great Ormond Street Hospital for Children NHS Foundation...撤销
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University Hospital ErlangenPervormance GmbH完全的
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Eunice Kennedy Shriver National Institute of Child...University of Washington未知
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare Diseases Clinical... 和其他合作者完全的红细胞生成性原卟啉症 | 环保计划 | XLP | X连锁原卟啉症 | XLPP | X 连锁显性红细胞生成性原卟啉病 | XLEPP | XLDP美国
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Nova Mentis Life Science CorpKGK Science Inc.暂停
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua Frase Foundation... 和其他合作者招聘中
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Ionis Pharmaceuticals, Inc.尚未招聘甲基 CpG 结合蛋白 2 (MECP2) 重复综合征
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI)完全的严重联合免疫缺陷 | 腺苷脱氨酶缺乏症 | 免疫系统紊乱 | 常染色体隐性遗传病 | 嘌呤核苷磷酸化酶缺乏症 | 缺乏 T 细胞和 B 细胞的严重联合免疫缺陷 | X连锁严重联合免疫缺陷美国
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bluebird bio终止脑肾上腺脑白质营养不良 (CALD) | 肾上腺脑白质营养不良 (ALD) | X 连锁肾上腺脑白质营养不良 (X-ALD)美国, 英国, 阿根廷, 加拿大, 德国, 意大利, 荷兰
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National Institute of Allergy and Infectious Diseases...完全的
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Rare Thyroid Therapeutics International ABVitaccess Ltd完全的
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bluebird bio主动,不招人脑肾上腺脑白质营养不良 (CALD) | 肾上腺脑白质营养不良 (ALD) | X 连锁肾上腺脑白质营养不良 (X-ALD)美国, 阿根廷, 澳大利亚, 巴西, 法国, 德国, 荷兰, 英国, 意大利
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State University of New York - Upstate Medical...终止
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD Foundation完全的
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)招聘中
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NightstaRx Ltd, a Biogen Company完全的
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis Therapeutics招聘中
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Universitair Ziekenhuis BrusselMarguerite - Marie Delacroix Foundation尚未招聘
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Assistance Publique - Hôpitaux de ParisBraintale尚未招聘X连锁肾上腺脑白质营养不良
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser Research Institute... 和其他合作者完全的
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NeuroVia, Inc.撤销
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Ionis Pharmaceuticals, Inc.招聘中
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRx可用的
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España Association完全的
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy Association完全的
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Bambino Gesù Hospital and Research InstituteAutour Des Williams; Acea未知
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of Child Health and... 和其他合作者完全的