搜索临床试验以:Mitochondrial depletion syndrome
总计38275个结果
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University of California, Los AngelesGilead Sciences完全的
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Wake Forest University Health Sciences终止
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Comenius UniversitySanatórium of Dr. Guhr, n.o.; Kaneka Pharma Europe N.V.完全的
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical Inc不再可用巴特综合症 | 线粒体三功能蛋白缺乏症 | 极长链酰基辅酶 A 脱氢酶 (VLCAD) 缺乏症 | 肉碱棕榈酰转移酶缺乏症(CPT1、CPT2) | 长链羟酰辅酶 A 脱氢酶缺乏症 | 糖原贮积障碍 | 丙酮酸羧化酶缺乏症 | 酰基辅酶 A 脱氢酶家族,成员 9,缺乏美国
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National Heart, Lung, and Blood Institute (NHLBI)完全的
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Medical College of WisconsinChildren's Hospital of Philadelphia完全的
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Khondrion BVDrug Research Unit Ghent, Belgium完全的
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University of Maryland, Baltimore撤销
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University of ArkansasSt. Christopher's Hospital for Children完全的
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Haukeland University HospitalOslo University Hospital; University Hospital of North Norway; The Research Council of Norway; Sykehuset... 和其他合作者完全的
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Federal Research Institute of Pediatric Hematology...完全的
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National Heart, Lung, and Blood Institute (NHLBI)完全的
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)终止
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research Trust未知
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St. Jude Children's Research Hospital完全的霍奇金淋巴瘤 | 骨髓增生异常综合征 (MDS) | 白血病,急性淋巴细胞性 (ALL) | 幼年型粒单核细胞白血病 (JMML) | 白血病,骨髓,急性(AML) | 白血病,骨髓,慢性(CML) | 血红蛋白尿,阵发性夜间 (PNH) | 淋巴瘤,非霍奇金 (NHL)美国
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Azienda Socio Sanitaria Territoriale degli Spedali...完全的小脑性共济失调 | 多系统萎缩 | 脊髓小脑共济失调 | 脊髓小脑退化 | 脊髓小脑性共济失调3 | 弗里德赖希共济失调 | 脊髓小脑性共济失调1型 | 脊髓小脑性共济失调2型 | 共济失调,脊髓小脑 | 共济失调,小脑 | 共济失调伴动眼神经失用症意大利
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Fundación para el Fomento de la Investigación Sanitaria...完全的
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy, Baylor College...完全的急性髓性白血病 | 急性淋巴细胞白血病 | 骨髓增生异常综合症 | 慢性粒细胞白血病 | 噬血细胞性淋巴组织细胞增多症 (HLH) | 非霍奇金淋巴瘤 | 家族性噬血细胞性淋巴组织细胞增生症 (FLH) | 病毒相关的噬血细胞综合症 (VAHS) | X 连锁淋巴增生性疾病 (XLP)美国
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Medical College of WisconsinChildren's Hospital and Health System Foundation, Wisconsin完全的
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Helsinki University Central HospitalGöteborg University; University of Iowa; University of Helsinki; Finnish Institute for Health and...完全的
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The University of Texas Health Science Center at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)完全的
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University of California, San DiegoBioMarin Pharmaceutical撤销
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Icahn School of Medicine at Mount SinaiColumbia University; New York Stem Cell Foundation Research Institute完全的临床孤立综合征 | 复发缓解型多发性硬化症 | 原发性进行性多发性硬化症 | 继发性进行性多发性硬化症美国
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University Hospital Hradec Kralove未知
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University of AarhusUniversity of Copenhagen完全的
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Medical University Innsbruck完全的肌筋膜疼痛 | 肌筋膜激痛点痛 | 疼痛,背部 | 疼痛,颈部 | 线粒体病理学
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Horizon Pharma USA, Inc.终止
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Children's Hospital of Philadelphia完全的
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Massachusetts General HospitalDana-Farber Cancer Institute终止
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University of ChileFondo Nacional de Desarrollo Científico y Tecnológico, Chile终止