氨基酸代谢,先天性错误的临床试验
总计4778个结果
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Travere Therapeutics, Inc.邀请报名
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BioMarin Pharmaceutical完全的苯丙酮尿症 (PKU) 或四氢生物蝶呤 (BH4) 缺乏症导致的高苯丙氨酸血症 (HPA)瑞典, 法国, 意大利, 西班牙, 德国, 荷兰, 奥地利, 斯洛伐克, 葡萄牙
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare...终止
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Travere Therapeutics, Inc.招聘中
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Hospital de Clinicas de Porto AlegreFundação de Amparo à Pesquisa do Estado do Rio Grande do Sul, Brazil暂停
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Children's Hospital Medical Center, Cincinnati完全的
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IRCCS Azienda Ospedaliero-Universitaria di BolognaUniversity of Bologna完全的
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National Institute of Neurological Disorders and...完全的
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Fondation Ophtalmologique Adolphe de Rothschild完全的
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National Center for Research Resources (NCRR)University of California, San Diego完全的同型半胱氨酸尿症
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Arcturus Therapeutics, Inc.招聘中
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S.LAB (SOLOWAYS)Center of New Medical Technologies; Triangel Scientific完全的高脂蛋白血症 | 高同型半胱氨酸血症俄罗斯联邦
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis Laboratories完全的
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Baylor College of MedicineSeattle Children's Hospital; University of California, San Francisco完全的
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Kaleido Biosciences终止
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Aeglea Biotherapeutics终止
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Academisch Medisch Centrum - Universiteit van Amsterdam...未知
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research Network; Office...完全的
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Ultragenyx Pharmaceutical Inc主动,不招人
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Netherlands Institute for Pigment DisordersAvita Medical完全的