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Kliniske forsøg med Kulhydratmetabolismeforstyrrelse
I alt 160411 resultater
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CENTOGENE GmbH RostockTrukket tilbageAlpha-Mannosidase B-mangel | Lysosomal Alpha B Mannosidose | Alpha-Mannosidase mangelIndien, Sri Lanka, Tyskland
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University Hospital, Strasbourg, FranceRekruttering
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VA New York Harbor Healthcare SystemMayo Clinic; New York UniversityUkendtOxalat, Primær Hyperoxaluri, MikrobiomForenede Stater
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JCR Pharmaceuticals Co., Ltd.RekrutteringMucopolysaccharidosis III-ATyskland
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CinnagenAfsluttetMucopolysaccharidosis type 1Iran, Islamisk Republik
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Sangamo TherapeuticsAfsluttet
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidoserForenede Stater
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation og andre samarbejdspartnereAfsluttetMucopolysaccharidosis Type IIIA | Mucopolysaccharidosis Type IIIBForenede Stater
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)AfsluttetPompes sygdomForenede Stater
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Genzyme, a Sanofi CompanyAfsluttetGlykogenopbevaringssygdom type IIForenede Stater, Taiwan, Israel, Det Forenede Kongerige, Frankrig
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Huazhong University of Science and TechnologyUkendtKardiovaskulær sygdom | Lactose malabsorptionKina
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Centre for Analytical Biochemistry and Biomedical...University of GiessenRekruttering
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National Taiwan University HospitalRekruttering
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National Taiwan University HospitalRekruttering
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Amicus TherapeuticsAktiv, ikke rekrutterendePompes sygdomForenede Stater, Holland, Det Forenede Kongerige, Australien, Tyskland, New Zealand
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...Afsluttet
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Asklepios Biopharmaceutical, Inc.Aktiv, ikke rekrutterende
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University of FloridaBioMarin PharmaceuticalAfsluttetPompes sygdomForenede Stater
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LMU KlinikumGenzyme, a Sanofi CompanyAfsluttetPompes sygdomTyskland, Taiwan, Italien
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Amicus TherapeuticsAfsluttetPompes sygdomFrankrig, Forenede Stater, Canada, Det Forenede Kongerige
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National Taiwan University HospitalAfsluttet
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National Taiwan University HospitalUkendt
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUkendtPompes sygdomSpanien
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National Taiwan University HospitalAfsluttet
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Amicus TherapeuticsAfsluttetGlykogenopbevaringssygdom type II | Pompes sygdomForenede Stater
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Baylor Research InstituteNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereUkendt
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Brain-Gut Research GroupAfsluttetIrritabelt tarmsyndrom | FruktoseintoleranceSchweiz
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University Children's Hospital, ZurichSanofiAfsluttet
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University of California, San FranciscoRekrutteringMPS IVA | MPS VIForenede Stater
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Ultragenyx Pharmaceutical IncAfsluttet
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Joyce FoxUltragenyx Pharmaceutical IncIkke længere tilgængeligMucopolysaccharidosis type 7Forenede Stater
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BioMarin PharmaceuticalAfsluttetMPS VIForenede Stater, Australien, Frankrig, Brasilien, Tyskland, Portugal, Det Forenede Kongerige
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRekruttering
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Genzyme, a Sanofi CompanyAktiv, ikke rekrutterende
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Amicus TherapeuticsLedig
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Duke UniversityAfsluttetGlykogenopbevaringssygdomForenede Stater
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Duke UniversityGenzyme, a Sanofi CompanyAfsluttet
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Duke UniversityAfsluttetPompes sygdomForenede Stater
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Duke UniversityAfsluttet
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Dwight Koeberl, M.D., Ph.D.Afsluttet
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University of California, IrvineGenzyme, a Sanofi CompanyAfsluttetPompes sygdomForenede Stater
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Amicus TherapeuticsAfsluttetPompes sygdomForenede Stater
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University of FloridaAfsluttet
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O & O Alpan LLCAfsluttet
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Centre Hospitalier de CayenneAfsluttet
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Genzyme, a Sanofi CompanyAfsluttet
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National Taiwan University HospitalUkendt
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Walter Reed Army Institute of Research (WRAIR)AfsluttetGlucosephosphat dehydrogenase mangel | FavismeForenede Stater
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SanofiRekruttering
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University of FloridaLacerta TherapeuticsAfsluttetPompes sygdomForenede Stater