先天性红细胞生成不良性贫血 1 型的临床试验
总计6268个结果
-
Jason Robert GotlibCelgene Corporation终止白血病 | 贫血 | 骨髓增生异常综合征 (MDS) | 急性髓系白血病 (AML)美国
-
Agios Pharmaceuticals, Inc.招聘中小儿丙酮酸激酶缺乏症 | 小儿溶血性贫血美国, 西班牙, 德国, 荷兰, 加拿大, 法国, 以色列, 瑞士, 意大利
-
Elizabeth Yang, MD, PhDUniversity of California, San Francisco; Global Blood Therapeutics; Pediatrix完全的
-
National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health (NIH)完全的
-
Children's Hospital Medical Center, Cincinnati完全的
-
Duke UniversityNational Institutes of Health (NIH)完全的
-
Assistance Publique - Hôpitaux de Paris完全的
-
St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Tennessee; Assisi Foundation完全的
-
University of California, San Francisco完全的镰状细胞性贫血症 | 血红蛋白病 | 地中海贫血 | 血液系统恶性肿瘤 | 免疫缺陷 | 范可尼贫血 | 非恶性疾病 | 遗传性先天性代谢错误美国
-
Novartis Pharmaceuticals完全的
-
St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)完全的
-
Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); St. Jude Children's Research Hospital; Tropical... 和其他合作者终止
-
Al-Neelain UniversityMilitary hospital; Ministry of Higher Education and Scientific Research, Republic of Sudan完全的
-
Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet Association招聘中铁代谢紊乱 | 镰状细胞性贫血症 | 地中海贫血 | 溶血;贫血,遗传性,由于酶紊乱 | 膜缺陷引起的贫血 | CDA | 铁粒幼细胞性贫血 | 体质性再生障碍性贫血 | 遗传性贫血西班牙
-
Hillhurst Biopharmaceuticals, Inc.National Heart, Lung, and Blood Institute (NHLBI)完全的
-
The University of Hong Kong完全的Homozygous αº-thalassemia | Hb Bart's Disease中国
-
Children's Hospital Medical Center, CincinnatiChildren's Hospital of Philadelphia; Emory University; Nemours Children's Health System尚未招聘
-
Hillhurst Biopharmaceuticals, Inc.National Heart, Lung, and Blood Institute (NHLBI)尚未招聘
-
Washington University School of MedicineNational Heart, Lung, and Blood Institute (NHLBI)完全的
-
Società Italiana Talassemie ed EmoglobinopatieAssociazione Italiana de Ematologia e Oncologia Pediatrica; Società Italiana di Medicina Trasfusionale...完全的
-
National Heart, Lung, and Blood Institute (NHLBI)终止
-
National Heart, Lung, and Blood Institute (NHLBI)终止