SCID的临床试验
总计1200个结果
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S.LAB (SOLOWAYS)Center of New Medical Technologies; Triangel Scientific完全的高脂蛋白血症 | 高同型半胱氨酸血症俄罗斯联邦
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Aeglea Biotherapeutics完全的
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, France完全的
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Children's National Research InstitutePatient-Centered Outcomes Research Institute; Eunice Kennedy Shriver National Institute of Child... 和其他合作者完全的
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Alexion Pharmaceuticals完全的溶酶体酸性脂肪酶缺乏症 | 缺乏 LAL | 胆固醇酯贮积症 (CESD)法国, 英国, 美国, 加拿大, 捷克语
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Academisch Medisch Centrum - Universiteit van Amsterdam...未知
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McGill University Health Centre/Research Institute...March of Dimes完全的
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CENTOGENE GmbH Rostock撤销代谢紊乱 | 酪氨酸病 | 肝肾酪氨酸血症 | 富马酰乙酰乙酸酶缺乏症 | 缺乏症德国, 斯里兰卡, 印度
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Alexion Pharmaceuticals完全的溶酶体酸性脂肪酶缺乏症 | 胆固醇酯贮积病(CESD) | 缺乏 LAL法国, 美国, 英国, 捷克语
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University Hospital, Clermont-Ferrand未知
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Travere Therapeutics, Inc.邀请报名
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Faculty Hospital Kralovske Vinohrady完全的阻塞性睡眠呼吸暂停 | 持续气道正压通气 | Fatty Acid Metabolism捷克语
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Netherlands Institute for Pigment DisordersAvita Medical完全的
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Travere Therapeutics, Inc.招聘中
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Hospital de Clinicas de Porto AlegreFundação de Amparo à Pesquisa do Estado do Rio Grande do Sul, Brazil暂停
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Charles University, Czech Republic未知
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Horizon Pharma Ireland, Ltd., Dublin Ireland完全的
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Second Affiliated Hospital of Nanchang UniversityPeking University First Hospital未知
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Shenzhen Ausa Pharmed Co.,LtdPeking University First Hospital; China Medical University, China; Fudan University; Chinese PLA... 和其他合作者未知
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National Center for Research Resources (NCRR)Baylor College of Medicine未知