搜索临床试验以:Brain Diseases, Metabolic, Inborn
总计48270个结果
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Khondrion BV尚未招聘线粒体疾病 | 线粒体 DNA tRNALeu(UUR) m.3243A | 母系遗传性糖尿病和耳聋 (MIDD) | 线粒体脑肌病、乳酸酸中毒和中风样发作 (MELAS)
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Takeda招聘中Dravet 综合症 (DS) | Lennox-Gastaut 综合症 (LGS)英国, 丹麦
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)尚未招聘脑淀粉样血管病
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin College招聘中图雷特综合症 | 抽动障碍 | 图雷特氏症 | 持续性抽动症 | 慢性运动抽动障碍 | 慢性声带抽动症 | 持续性运动抽动障碍 | 持续性发声抽动障碍美国
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Tisento Therapeutics尚未招聘
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Takeda尚未招聘Dravet 综合症 (DS) | Lennox-Gastaut 综合症 (LGS)
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University College, LondonLondon School of Hygiene and Tropical Medicine; King's College London; University College London... 和其他合作者招聘中
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University of Utah招聘中
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The First Affiliated Hospital of Zhejiang Chinese...招聘中
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Jirair Krikor BedoyanUltragenyx Pharmaceutical Inc招聘中
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Rigshospitalet, Denmark尚未招聘脑部疾病 | 先天性遗传病 | 新陈代谢,先天性错误 | 脑部疾病,代谢 | 苯丙酮尿症 | 脑部疾病,代谢性,先天性 | 氨基酸代谢,先天性错误 | 代谢性疾病丹麦
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham Women's and Children...尚未招聘黑尿症 | 同型半胱氨酸;代谢紊乱 | 酪氨酸血症,I 型 | 酪氨酸血症,II 型 | 酪氨酸血症,III 型 | MSUD(枫糖浆尿病)
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Specila hospital for cerebral palsy and developmental...FRAXA Research Foundation招聘中
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.招聘中
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Université du Québec à ChicoutimiMcGill University; Université de Sherbrooke; University of Alberta; University of Calgary; Laval University 和其他合作者招聘中
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre hospitalier universitaire... 和其他合作者尚未招聘脆性 X 综合征
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iECURE, Inc.招聘中尿素循环障碍,先天性 | 鸟氨酸转氨甲酰酶缺乏症 | 鸟氨酸转氨甲酰酶缺乏症 | 鸟氨酸氨基甲酰转移酶缺乏症(疾病)英国
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PTC Therapeutics招聘中
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Travere Therapeutics, Inc.招聘中
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.招聘中
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)招聘中