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Ensayos clínicos patrocinados por ORDR
Total 314 resultados
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National Institute of Neurological Disorders and...Jefferson Medical College of Thomas Jefferson UniversityTerminadoSíndrome de TurnerEstados Unidos
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National Institute of Diabetes and Digestive and...Southwest Pediatric Nephrology Study GroupTerminado
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonDesconocidoSíndrome de Wiskott-Aldrich | Síndrome de Deficiencia de Adhesión de Leucocitos | Agammaglobulinemia ligada al cromosoma X | Síndrome de hiper IgM ligado al cromosoma XEstados Unidos
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityTerminadoSíndrome de Rett
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Eunice Kennedy Shriver National Institute of Child...Nationwide Children's HospitalTerminado
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National Institute of Neurological Disorders and...Jefferson Medical College of Thomas Jefferson UniversityTerminadoSíndrome de TurnerEstados Unidos
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Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)TerminadoDeficiencia de 21-hidroxilasaEstados Unidos, Brasil
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineTerminadoSíndrome de Rett
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineTerminadoSíndrome de Rett
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Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminadoEnfermedad por deficiencia de ornitina transcarbamilasa
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... y otros colaboradoresTerminadoSíndrome de Andersen-TawilEstados Unidos
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Eunice Kennedy Shriver National Institute of Child...Children's Hospital of PhiladelphiaTerminadoSíndrome de Dificultad Respiratoria
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID); Rockefeller UniversityTerminadoInfecciones por VIH | Infecciones por micobacterias | Tuberculosis
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... y otros colaboradoresTerminadoEnfermedades Cerebrales Metabólicas Congénitas | Deficiencia de ornitina transcarbamilasa | Trastorno del ciclo de la ureaEstados Unidos
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National Center for Research Resources (NCRR)Johns Hopkins University; National Institute of Neurological Disorders and Stroke...Terminado
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); University of...TerminadoEstudio de fase III, aleatorizado, doble ciego, de prednisona para la distrofia muscular de DuchenneDistrofia muscular de Duchenne
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Laval UniversityCentre Interdisciplinaire de Recherche en Réadaptation et Intégration Sociale; Fonds de la Recherche en Santé du Québec y otros colaboradoresTerminado
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network y otros colaboradoresReclutamientoArteritis de células gigantes | Poliangitis microscópica | Poliarteritis Nodosa | Arteritis de Takayasu | Granulomatosis eosinofílica con poliangitis (Churg-Strauss) | Granulomatosis con poliangitis (de Wegener)Estados Unidos, Canadá, Pavo
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of Rare Diseases...TerminadoArteritis de células gigantes | Arteritis de TakayasuEstados Unidos, Canadá
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network y otros colaboradoresTerminadoGranulomatosis de WegenerEstados Unidos
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National Center for Research Resources (NCRR)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rockefeller UniversityTerminadoEpidermólisis Bullosa
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network y otros colaboradoresTerminadoArteritis TemporalEstados Unidos, Canadá
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network y otros colaboradoresTerminadoPoliarteritis NodosaEstados Unidos, Canadá
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National Center for Research Resources (NCRR)Northwestern University; National Institute of Arthritis and Musculoskeletal...TerminadoLupus eritematoso sistémico
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network y otros colaboradoresTerminadoPoliangitis microscópica | Granulomatosis con poliangeítis | De WegenerEstados Unidos, Canadá
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network y otros colaboradoresTerminadoDeterminación de biomarcadores de actividad de la enfermedad en individuos con arteritis de TakayasuArteritis de TakayasuEstados Unidos, Canadá
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National Center for Research Resources (NCRR)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Stanford UniversityTerminadoEsclerosis sistemica
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Laval UniversityCIRRIS (Center for Interdisciplinary Research in Rehabilitation and Social... y otros colaboradoresTerminadoEficacia de los ejercicios de control motor supervisados en las tendinopatías del manguito rotadorSíndrome de pinzamiento del hombro | Tendinopatía del manguito rotador del hombroCanadá
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI); National Center for Research... y otros colaboradoresTerminadoDiscinesia ciliar primariaEstados Unidos, Canadá
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID); University of...TerminadoHistoplasmosis | Esporotricosis | Blastomicosis
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National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...TerminadoCálculos renales | Hipercalciuria
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National Center for Research Resources (NCRR)University of California, Los Angeles; National Institute of Neurological Disorders...TerminadoEnfermedad de Huntington
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National Center for Research Resources (NCRR)University of California, Los Angeles; National Institute of Neurological Disorders...Terminado
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID); University of...TerminadoHistoplasmosis | Esporotricosis | Blastomicosis
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National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...TerminadoEstudio aleatorizado de fase III de ursodiol con vs sin metotrexato para la cirrosis biliar primariaCirrosis Hepática Biliar
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National Center for Research Resources (NCRR)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); University of TexasTerminado
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); National Center for Advancing Translational Sciences (NCATS) y otros colaboradoresReclutamientoVasculitis IgA | Púrpura de Henoch-Schönlein | Poliarteritis Nodosa Cutánea | Vasculitis cutánea primariaEstados Unidos, Canadá, Japón
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network y otros colaboradoresTerminadoArteritis de TakayasuEstados Unidos, Canadá
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); National Center for Advancing Translational Sciences (NCATS) y otros colaboradoresReclutamientoArteritis de células gigantes | Poliangitis microscópica | Síndrome de Churg-Strauss | Poliarteritis Nodosa | Granulomatosis eosinofílica con poliangitis | Púrpura de Henoch-Schonlein | Arteritis de Takayasu | Aortitis | Vasculitis IgA | Granulomatosis con poliangitis (de Wegener) | Vasculitis cutáneaEstados Unidos, Canadá
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... y otros colaboradoresTerminadoObesidad | Síndrome de Prader-WilliEstados Unidos
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Office of Rare... y otros colaboradoresInscripción por invitaciónSíndrome de Presagio | Disgenesia reticular | Inmunodeficiencia Combinada Severa (SCID) | XSCID | SCID con fugas | SCID de la ADAEstados Unidos, Canadá
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); Icahn School...TerminadoEnfermedad de Parkinson
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... y otros colaboradoresTerminadoProtoporfiria eritropoyética | PPE | XLP | Protoporfiria ligada al cromosoma X | XLPP | Protoporfiria eritropoyética dominante ligada al cromosoma X | XLEPP | XLDPEstados Unidos
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National Center for Research Resources (NCRR)Eunice Kennedy Shriver National Institute of Child Health and Human Development... y otros colaboradoresTerminado
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development... y otros colaboradoresTerminadoMetabolismo de aminoácidos, errores congénitos | Trastornos del ciclo de la urea | Aciduria argininosuccínicaEstados Unidos
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Icahn School of Medicine at Mount SinaiEunice Kennedy Shriver National Institute of Child Health and Human Development... y otros colaboradoresTerminadoSíndrome de Exceso Aparente de MineralocorticoidesEstados Unidos, Brasil, Francia
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Children's Hospital Medical Center, CincinnatiNational Institute of Allergy and Infectious Diseases (NIAID); National Institute... y otros colaboradoresTerminadoCaracterísticas de la gastritis, enteritis y colitis eosinofílica en una cohorte de sitios múltiplesGastritis Eosinofílica | Gastroenteritis Eosinofílica | Esofagitis eosinofílica | Colitis eosinofílicaEstados Unidos
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Children's Hospital Medical Center, CincinnatiNational Institute of Allergy and Infectious Diseases (NIAID); National Institute... y otros colaboradoresTerminadoGastroenteritis EosinofílicaEstados Unidos
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Children's Hospital Medical Center, CincinnatiNational Institute of Allergy and Infectious Diseases (NIAID); National Institute... y otros colaboradoresTerminadoEsofagitis eosinofílicaEstados Unidos
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Children's Hospital Medical Center, CincinnatiNational Institute of Allergy and Infectious Diseases (NIAID); National Institute... y otros colaboradoresTerminadoEsofagitis eosinofílicaEstados Unidos