- ICH GCP
- Registro degli studi clinici negli Stati Uniti
- Search trials
Cerca studi clinici per: genetic diseases and dysmorphic syndromes
Totale 478820 risultati
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Eunice Kennedy Shriver National Institute of Child...ReclutamentoDisturbo dello spettro autistico | Sindrome dell'X fragile | Ritardo dello sviluppo | Disordine genetico | Disturbo di AspergerStati Uniti
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Eunice Kennedy Shriver National Institute of Child...CompletatoMalattia metabolica | Disordine geneticoStati Uniti
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National Institute of Diabetes and Digestive and...University of FloridaCompletato
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UCSF Benioff Children's Hospital OaklandCompletatoAnemia falciforme | Necrosi ossea avascolareStati Uniti
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Susan P. PerrineIcahn School of Medicine at Mount Sinai; University of Illinois at Chicago; Boston... e altri collaboratoriCompletatoAnemia falciforme | Ulcere cutaneeStati Uniti
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FDA Office of Orphan Products DevelopmentUniversity of North CarolinaCompletato
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Children's Hospital Medical Center, CincinnatiCompletatoFibrosi cisticaStati Uniti, Italia
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FDA Office of Orphan Products DevelopmentMedical University of South CarolinaCompletato
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompletato
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University of North CarolinaCompletato
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FDA Office of Orphan Products DevelopmentCochlearCompletato
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FDA Office of Orphan Products DevelopmentCompletatoFibrosi cistica | Infezione batterica
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University of North CarolinaCompletatoAnemia falciformeStati Uniti
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Ohio State UniversityCompletatoDistrofia muscolare, facioscapolo-omerale
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University of IowaCompletato
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Boston Children's HospitalCompletatoAnemia falciformeStati Uniti
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FDA Office of Orphan Products DevelopmentSciClone PharmaceuticalsCompletato
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University of North CarolinaCompletatoOsteoporosi | Fibrosi cisticaStati Uniti
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University of PennsylvaniaTerminatoMalattia da carenza di ornitina transcarbamilasi
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Mast Therapeutics, Inc.CytRxCompletato
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University of Alabama at BirminghamNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completato
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University of Alabama at BirminghamCompletato
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Fairview University Medical CenterTerminatoSindromi da deficit immunologico | Immunodeficienza variabile comune | Immunodeficienza combinata grave | Malattia granulomatosa cronica | Linfoistiocitosi emofagocitica | Sindrome di Wiskott-Aldrich | Malattia del trapianto contro l'ospite | Agammaglobulinemia legata all'X | Sindrome di Chediak-Higashi | Sindrome emofagocitica associata a virus e altre condizioniStati Uniti
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University of UtahCompletatoFibrosi cisticaStati Uniti
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National Institute of Neurological Disorders and...Jefferson Medical College of Thomas Jefferson UniversityCompletato
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Fred Hutchinson Cancer CenterCompletatoAnemia falciformeStati Uniti
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University of UtahCompletatoFibrosi cisticaStati Uniti
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Herbert Irving Comprehensive Cancer CenterCompletato
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Boston UniversityCompletatoBeta-talassemiaStati Uniti, Regno Unito
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National Center for Research Resources (NCRR)Indiana University School of MedicineCompletato
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National Institute of Neurological Disorders and...Baylor College of MedicineCompletatoSindrome di Prader-Willi | Sindrome di DiGeorge | Sindrome di Williams | Sindrome di Angelmann | Sindrome di Smith-Magenis | Anomalie cromosomiche | Sindrome di ShprintzenStati Uniti
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National Center for Research Resources (NCRR)Children's Hospital Medical Center, CincinnatiSconosciutoMalattie gastrointestinali | Fibrosi cistica | ColestasiStati Uniti
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National Center for Research Resources (NCRR)Northwestern UniversityCompletatoEpidermolisi bollosa acquisita
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletatoTrombocitopenia | Errori congeniti del metabolismo | Leucodistrofia metacromatica | Anemia di Fanconi | Talassemia Maggiore | Aplasia eritrocitaria puraStati Uniti
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National Center for Research Resources (NCRR)Yale UniversityCompletato
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National Center for Research Resources (NCRR)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rockefeller UniversityCompletatoEpidermolisi Bollosa
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National Center for Research Resources (NCRR)Indiana University School of MedicineSconosciuto
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National Center for Research Resources (NCRR)University of North CarolinaCompletatoFibrosi cistica | Atypical Mycobacterium Infection
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National Center for Research Resources (NCRR)University of PittsburghTerminatoDeficit di alfa 1-antitripsinaStati Uniti
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National Center for Research Resources (NCRR)University of RochesterCompletatoSpondilite anchilosante
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National Center for Research Resources (NCRR)University of UtahTerminato
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Fairview University Medical CenterSconosciutoMucopolisaccaridosi I | Malattia di Niemann-Pick | Mucopolisaccaridosi VI | Malattia di Wolmann | Adrenoleucodistrofia | Leucodistrofia metacromatica | Complicanze polmonari | Fucosidosi | Leucodistrofia a cellule globoide | Malattia di Gaucher | Mannosidosi | Malattia cellulareStati Uniti
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National Center for Research Resources (NCRR)Ann & Robert H Lurie Children's Hospital of ChicagoCompletatoDifetti cardiaci, congeniti | Tetralogia di Fallot | Stenosi della valvola polmonare | Ipoparatiroidismo | Atresia polmonare | Difetti cardiaci conotruncali
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National Center for Research Resources (NCRR)University of MichiganCompletato
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletatoStenosi | IstiocitomaStati Uniti
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National Center for Research Resources (NCRR)Vanderbilt University Medical CenterCompletato
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National Center for Research Resources (NCRR)Baylor College of MedicineCompletato
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National Center for Research Resources (NCRR)Yale UniversityCompletato
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National Center for Research Resources (NCRR)Children's Hospital of PhiladelphiaCompletatoOsteoporosi | Osteopenia | Talassemia Maggiore
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National Center for Research Resources (NCRR)University of PennsylvaniaCompletato