Clinical Trials on 先天性代謝異常症 in United States
合計3224件
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University of PennsylvaniaNorthwestern University; Family Heart Foundation招待による登録
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VA Office of Research and Development完了
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.積極的、募集していない
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Bellicum Pharmaceuticals利用できないハーラー症候群 | 先天性代謝異常症 | 異染性白質ジストロフィー | 遺伝性代謝障害 | リソソーム蓄積症アメリカ
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Jerry Vockley, MD, PhDAcer Therapeutics Inc.募集
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical Inc募集
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Northwestern UniversityUniversity of Pennsylvania; Family Heart Foundation招待による登録
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Emory UniversityKaneka Medical America LLC完了
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Geisinger ClinicNational Heart, Lung, and Blood Institute (NHLBI)招待による登録
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University of Texas Southwestern Medical Center完了
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Alexion Pharmaceuticals完了
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Vanderbilt University Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)募集
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National Heart, Lung, and Blood Institute (NHLBI)完了
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Northwestern UniversityUniversity of Pennsylvania; Family Heart Foundation完了
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Alexion Pharmaceuticalsマーケティング承認済み
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Alexion Pharmaceuticals完了
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)一時停止
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Origin Biosciences完了モリブデン補因子欠乏症アメリカ, オーストラリア, イギリス, ドイツ, オランダ, 七面鳥
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Boston Children's HospitalWellth Inc.; MMAS-8 with permission from Dr Donald Morisky. as written below募集
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National Center for Research Resources (NCRR)Oregon Health and Science Universityわからない
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The Familial Hypercholesterolemia Foundation募集
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University of PennsylvaniaLancaster General Hospital; The Familial Hypercholesterolemia Foundation完了
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Alexion Pharmaceuticals完了
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National Human Genome Research Institute (NHGRI)完了未診断疾患 | ヘルシーボランティア(一般的に発育中の子供を持つ大人) | 遺伝性神経変性疾患 | 遺伝性代謝障害(先天性代謝異常症) | アルツハイマー病および関連する認知症アメリカ
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University of Wisconsin, MadisonJohns Hopkins University; National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) と他の協力者招待による登録
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Alexion Pharmaceuticals完了
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University of Wisconsin, MadisonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Stanford University完了
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National Human Genome Research Institute (NHGRI)募集
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University of PennsylvaniaRegeneron Pharmaceuticals完了
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Sheffield Teaching Hospitals NHS Foundation TrustNational Institute for Health Research, United Kingdom; Alexion Pharmaceuticals, Inc.完了
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Vanderbilt University Medical CenterHarvard University募集
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of Sheffield積極的、募集していない
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Boston Children's HospitalBrigham and Women's Hospital完了