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뇌 질환, 대사에 대한 임상 시험
총 379517 건
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Lysosomal and Rare Disorders Research and Treatment...모병
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare Diseases Clinical Research Network종료됨
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Tulane University School of MedicineBioMarin Pharmaceutical완전한
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Aeglea Biotherapeutics완전한
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The Hospital for Sick ChildrenBioMarin Pharmaceutical완전한
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IntraBio Inc완전한
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, Worcester모집하지 않고 적극적으로
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National Institute of Neurological Disorders and...완전한
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Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical Sciences모병
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The Hospital for Sick ChildrenActelion완전한
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Centre for Analytical Biochemistry and Biomedical...University of Giessen모병
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National Human Genome Research Institute (NHGRI)모병
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Lianyungang Oriental HospitalThe First People's Hospital of Lianyungang알려지지 않은
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Travere Therapeutics, Inc.모집하지 않고 적극적으로
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Ultragenyx Pharmaceutical Inc완전한
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Genzyme, a Sanofi Company모집하지 않고 적극적으로
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Baylor Research InstituteTexas Scottish Rite Hospital for Children빼는
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Horizon Therapeutics, LLC완전한우레아 순환 장애미국, 스페인, 이탈리아, 스위스
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Horizon Pharma Ireland, Ltd., Dublin Ireland완전한
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Amicus Therapeutics모집하지 않고 적극적으로폼페병미국, 네덜란드, 영국, 호주, 독일, 뉴질랜드
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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LMU KlinikumGenzyme, a Sanofi Company완전한
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National Taiwan University Hospital알려지지 않은
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Genzyme, a Sanofi Company완전한