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유전병, 선천적에 대한 임상 시험
총 382505 건
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare Diseases Clinical Research Network 그리고 다른 협력자들완전한아미노산 대사, 선천적 오류 | 우레아 순환 장애 | 아르기니노숙신산뇨증미국
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Leadiant Biosciences, Inc.모집하지 않고 적극적으로
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National Heart, Lung, and Blood Institute (NHLBI)완전한
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome Medical종료됨
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Novartis Pharmaceuticals완전한
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Amsterdam Molecular TherapeuticsICON plc종료됨
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Sanofi모병
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Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTD모병
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APR Applied Pharma Research s.a.모병
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University Children's Hospital, ZurichUniversity Children's Hospital Basel; UChildrenVienna; Insel Gruppe AG, University Hospital...모병
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University Hospital, Lille아직 모집하지 않음
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Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken Reutlingen완전한
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Ludwig-Maximilians - University of MunichEuropean Union완전한
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Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin Pharmaceutical완전한
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital완전한
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University of Missouri-ColumbiaBioMarin Pharmaceutical완전한
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BioMarin Pharmaceutical완전한
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Emory UniversityAtlanta Clinical and Translational Science Institute완전한
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The University of Texas Health Science Center,...BioMarin Pharmaceutical종료됨
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital완전한
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The University of Texas Health Science Center,...BioMarin Pharmaceutical완전한
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Shoji YanoBioMarin Pharmaceutical완전한
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BioMarin Pharmaceutical완전한
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Neurogene Inc.종료됨
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Imperial College London Diabetes Centre알려지지 않은멘델 장애 | 유전 장애 | 새로운 돌연변이 | 유전 장애 | 새로운 돌연변이 | 유전병 | 단일 유전자 결함아랍 에미리트