X-koblet kreatinmangel的临床试验
总计1831个结果
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Bambino Gesù Hospital and Research InstituteAutour Des Williams; Acea未知
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research Trust未知
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Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical Center完全的
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); National... 和其他合作者完全的
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Rush University Medical CenterEmory University邀请报名结节性硬化症 | 脆性 X 综合征 | 雷特综合症 | 多发性错构瘤综合征 | 天使综合症 | 肌酸缺乏症,X 连锁 | 端粒 22Q13 单体综合征 | 染色体 15Q,部分缺失美国
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The University of Hong KongQueen Mary Hospital, Hong Kong; Kowloon Hospital, Hong Kong; Castle Peak Hospital; Zhejiang Provincial...完全的
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI)完全的严重联合免疫缺陷 | 腺苷脱氨酶缺乏症 | 免疫系统紊乱 | 常染色体隐性遗传病 | 嘌呤核苷磷酸化酶缺乏症 | 缺乏 T 细胞和 B 细胞的严重联合免疫缺陷 | X连锁严重联合免疫缺陷美国
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)邀请报名
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - Italy完全的
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Newron Pharmaceuticals SPA终止
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University of California, Los AngelesLAC+USC Medical Center; Los Angeles Department of Health Services; American Board of Internal...完全的核磁共振 | 背疼 | CT扫描 | X光片 | 临床决策支持工具
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of Child Health and... 和其他合作者完全的
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); National... 和其他合作者完全的
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Columbia UniversityAlmond Board of California完全的
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Edimer Pharmaceuticals完全的X连锁少汗性外胚层发育不良美国, 英国, 法国, 德国, 意大利
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Edimer Pharmaceuticals完全的
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Edimer PharmaceuticalsNational Foundation of Ectodermal Dysplasia完全的
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Wageningen UniversityUnilever R&D; Netherlands Heart Foundation完全的
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta University; University... 和其他合作者招聘中
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Great Ormond Street Hospital for Children NHS Foundation...撤销
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National Institute of Allergy and Infectious Diseases...完全的
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Eunice Kennedy Shriver National Institute of Child...终止
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare Diseases Clinical... 和其他合作者完全的红细胞生成性原卟啉症 | 环保计划 | XLP | X连锁原卟啉症 | XLPP | X 连锁显性红细胞生成性原卟啉病 | XLEPP | XLDP美国
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University Hospital, Clermont-FerrandInstitut National de la Recherche Agronomique未知
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Universitair Ziekenhuis BrusselMarguerite - Marie Delacroix Foundation尚未招聘
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Bio Products Laboratory完全的常见变异型免疫缺陷 | 原发性免疫缺陷病 | 高 IgM 综合症 | X连锁无丙种球蛋白血症美国, 英国, 匈牙利
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD Foundation完全的
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Joseph Calabrese, MDTakeda Pharmaceuticals North America, Inc.完全的
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Assistance Publique - Hôpitaux de ParisBraintale尚未招聘X连锁肾上腺脑白质营养不良
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser Research Institute... 和其他合作者完全的