X 连锁肌酸缺乏症的临床试验
总计1565个结果
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Lundquist Institute for Biomedical Innovation at...主动,不招人
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI); National Marrow... 和其他合作者完全的慢性肉芽肿病 | 噬血细胞性淋巴组织细胞增生症 | 白细胞粘附缺陷 | 慢性活动性 EB 病毒感染 | HIGM-1 | IPEX美国, 加拿大
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Wuerzburg University HospitalKyowa Kirin, Inc.完全的
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National Institute of Allergy and Infectious Diseases...招聘中
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National Institute of Allergy and Infectious Diseases...邀请报名
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SwanBio Therapeutics, Inc.招聘中
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Eunice Kennedy Shriver National Institute of Child...终止
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Kyowa Kirin Pharmaceutical Development Ltd完全的
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment Consortium (PIDTC)完全的
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The Korean Society of Pediatric Hematology Oncology完全的
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Grifols Therapeutics LLC完全的
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National Institute of Arthritis and Musculoskeletal...完全的
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University Hospital, MontpellierAgence de La Biomédecine主动,不招人
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital NHS Foundation... 和其他合作者完全的
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NightstaRx Ltd, a Biogen Company完全的
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TakedaTakeda Development Center Americas, Inc.招聘中
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National Institute of Neurological Disorders and...招聘中
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical Inc不再可用巴特综合症 | 线粒体三功能蛋白缺乏症 | 极长链酰基辅酶 A 脱氢酶 (VLCAD) 缺乏症 | 肉碱棕榈酰转移酶缺乏症(CPT1、CPT2) | 长链羟酰辅酶 A 脱氢酶缺乏症 | 糖原贮积障碍 | 丙酮酸羧化酶缺乏症 | 酰基辅酶 A 脱氢酶家族,成员 9,缺乏美国
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National Institute for Mother and Child Health...Marie Curie Emergency Children's Hospital, Bucharest; Victor Gomoiu Children's Hospital, Bucharest招聘中
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Fondazione TelethonOspedale San Raffaele完全的
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Federal Research Institute of Pediatric Hematology...未知造血干细胞移植 | Wiskott-Aldrich 综合症 | 移植失败俄罗斯联邦
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Medical University of Graz完全的
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Lundquist Institute for Biomedical Innovation at...终止
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Kiora Pharmaceuticals, Inc.招聘中
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Center for Eye Research AustraliaAustralian National University; Commonwealth Scientific and Industrial Research Organisation... 和其他合作者邀请报名
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical Emas完全的
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Mobius Medical Pty Ltd.University of Melbourne; Australian National University; Centre for Eye Research Australia; Bionics... 和其他合作者完全的