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X-연관 림프증식성 증후군 2에 대한 임상 시험
총 3524 건
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National MPS SocietyMediResource Inc.종료됨점액다당증 I | 뮤코다당증 II | 뮤코다당류증 | 점액다당증 VI | 점액다당증 IV미국
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Gillette Children's Specialty Healthcare완전한
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University of Seville; Hospital... 그리고 다른 협력자들모집하지 않고 적극적으로
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.완전한
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Wuerzburg University HospitalKyowa Kirin, Inc.모집하지 않고 적극적으로
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Minoryx Therapeutics, S.L.모집하지 않고 적극적으로부신백질이영양증스페인, 미국, 헝가리, 프랑스, 독일, 이탈리아, 네덜란드, 영국
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)종료됨
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Rush University Medical Center완전한
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Lev-Hasharon Mental Healtlh Center알려지지 않은
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Minoryx Therapeutics, S.L.모병대뇌부신백질디스트로피(cALD)미국, 브라질, 아르헨티나
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Poxel SA아직 모집하지 않음
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases Clinical...모병
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bluebird bio완전한대뇌부신백질이영양증(CALD)미국, 프랑스, 독일, 이탈리아, 네덜란드, 영국
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Manchester University NHS Foundation Trust완전한
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bluebird bio완전한대뇌부신백질이영양증(CALD)미국, 독일, 아르헨티나, 호주, 프랑스, 영국
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Assistance Publique - Hôpitaux de ParisCentre National de la Recherche Scientifique, France완전한
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University Hospital Heidelberg완전한뮤코다당증 I형 | 뮤코다당증 II형 | 대처 행동 | 뮤코다당증 III형 | 행동 장애독일
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Masonic Cancer Center, University of Minnesota빼는
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.완전한
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic University알려지지 않은
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National Center for Research Resources (NCRR)Ohio State University완전한근위축성 측삭 경화증 | 척추 근육 위축 | Spinobulbar 근육 위축
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University of Wisconsin, MadisonAmerican Heart Association; American Diabetes Association완전한
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University of ConnecticutCalifornia Table Grape Commission완전한
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University of East AngliaHarvard School of Public Health (HSPH)완전한
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University of PennsylvaniaEli Lilly and Company완전한
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Laval UniversityCanadian Institutes of Health Research (CIHR)완전한
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University of WashingtonPfizer; National Institutes of Health (NIH); Northwest Lipid Research Clinic알려지지 않은
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University of UlmSunesis Pharmaceuticals완전한급성 골수성 백혈병 | 과도한 모세포-2가 있는 골수이형성 증후군(MDS-EB-2)독일
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Stanford UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of California, Los Angeles; National Institutes of Health (NIH) 그리고 다른 협력자들완전한
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Taiyuan Central Hospital of Shanxi Medical University완전한
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Chinese Academy of SciencesCalifornia Walnut Commission완전한
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Hannover Medical School완전한
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Health Enhancement Products, Inc.University of Yaounde완전한
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Mads Peter Godtfeldt StemmerikEdgewise Therapeutics, Inc.완전한
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National Institute of Allergy and Infectious Diseases...모병