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Kliniske studier sponset av FDA Office of Orphan Products Development
Totalt 141 resultater
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University of MichiganFullført
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University of PennsylvaniaAvsluttetOrnithine Transcarbamylase Deficiency Disease
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University of TennesseeFDA Office of Orphan Products DevelopmentFullført
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University of ArizonaFDA Office of Orphan Products DevelopmentAvsluttetCoccidioidomycosisForente stater
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Boston Children's HospitalFDA Office of Orphan Products DevelopmentAktiv, ikke rekrutterende
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentFullførtEn sikkerhets- og effektstudie av AEGR-733 for å behandle homozygot familiær hyperkolesterolemi (FH)Homozygot familiær hyperkolesterolemiForente stater, Canada, Italia, Sør-Afrika
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National Jewish HealthFullførtFase II-studie av amithiozon (thiacetazon) for pasienter med Mycobacterium Avium Complex lungesykdomMycobacterium Avium-intracellulare infeksjon
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Johns Hopkins UniversityFullført
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Holles Laboratories, Inc.FullførtTilbakefall | Korneal sykdommerForente stater
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NeuroHealing Pharmaceuticals Inc.FDA Office of Orphan Products DevelopmentSuspendert
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The Cleveland ClinicFullført
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FDA Office of Orphan Products DevelopmentBoston Children's HospitalFullført
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Johns Hopkins UniversityFullførtEpilepsi | Cysticercosis
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Bellus Health IncFDA Office of Orphan Products DevelopmentFullførtGastrointestinale sykdommer | Nyresykdommer | Leddgikt | Nefrotisk syndrom | Sekundær (AA) amyloidose | Familiært middelhavssyndromForente stater, Israel, Finland, Frankrike, Italia, Litauen, Nederland, Polen, Den russiske føderasjonen, Spania, Tyrkia, Storbritannia
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Boston Children's HospitalFDA Office of Orphan Products DevelopmentAvsluttet
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Emmaus Medical, Inc.FDA Office of Orphan Products DevelopmentFullførtSigdcelleanemi | ThalassemiForente stater
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IWK Health CentreFullførtPertussis | Kikhoste
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Ohio State UniversityFullførtMuskeldystrofi, Facioscapulohumeral
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FDA Office of Orphan Products DevelopmentLeadiant Biosciences, Inc.Fullført
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Boston Children's HospitalFullførtSigdcelleanemiForente stater
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The Cleveland ClinicAvsluttet
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Seattle Children's HospitalFullførtSmerte | Spedbarn, nyfødte, sykdommer
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Massachusetts General HospitalFullført
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University of North CarolinaFullført
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FDA Office of Orphan Products DevelopmentChildren's Hospital of PhiladelphiaFullført
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FDA Office of Orphan Products DevelopmentUniversity of North CarolinaFullført
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Children's Hospital of PhiladelphiaFullført
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Children's Hospital of PhiladelphiaFullført
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Medical College of WisconsinFDA Office of Orphan Products DevelopmentAvsluttetHemangiomaForente stater
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University of North CarolinaFullførtSigdcelleanemiForente stater
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FDA Office of Orphan Products DevelopmentUniversity of Massachusetts, WorcesterFullførtJuvenil revmatoid artritt
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University of North CarolinaFullførtOsteoporose | Cystisk fibroseForente stater
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Children's Hospital Los AngelesFullførtTrombose | Heparin-indusert trombocytopeniForente stater
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Brigham and Women's HospitalFullførtErytropoetisk protoporfyri
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityFullført
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityFullført
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Case Western Reserve UniversityAvsluttet
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M.D. Anderson Cancer CenterFullførtLymfoproliferative lidelser | Leukemi | Hematologiske neoplasmer | Leukemi, lymfatisk, kroniskForente stater
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George BrewerFDA Office of Orphan Products DevelopmentFullførtPrimær biliær cirrhoseForente stater
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FDA Office of Orphan Products DevelopmentUniversity of Illinois at ChicagoFullført
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University of California, San DiegoFullførtMelkeacidoseForente stater
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Memorial Hospital of Rhode IslandFullført
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Retina Foundation of the SouthwestFullført
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FDA Office of Orphan Products DevelopmentMedical University of South CarolinaFullført
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California Department of Health ServicesFullførtBotulisme | SpedbarnsbotulismeForente stater
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentFullførtPectus ExcavatumForente stater
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentAvsluttetVedvarende epiteldefekter i hornhinnen
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State University of New YorkFullført
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State University of New YorkFullførtDupuytrens kontraktForente stater
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Children's Hospital Medical Center, CincinnatiFullførtTourettes syndrom