无义突变杜氏肌营养不良症的临床试验
总计856个结果
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Norwegian School of Sport SciencesUniversity of Oslo; Oslo University Hospital; University of Copenhagen; University of Southern Denmark 和其他合作者完全的
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University Hospital, BonnForschungszentrum Juelich; The Marigold Foundation; Life and Brain Center Bonn完全的强直性营养不良 1 | 强直性营养不良 2
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Grete Andersen, MDAP Moeller Foundation; The Danish Rheumatism Association; Aase and Ejnar Danielsens Foundation; The...完全的
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Rigshospitalet, DenmarkFunding: Toyota Foundation; Funding: Hede Nielsen Foundation; Funding: Grosserer L. F. Foghts... 和其他合作者主动,不招人
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Vertex Pharmaceuticals Incorporated招聘中
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Dyne Therapeutics招聘中强直性营养不良 1 型 (DM1)英国, 法国, 荷兰, 意大利, 德国, 新西兰
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Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University of Minnesota; Nationwide... 和其他合作者招聘中
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Sarepta Therapeutics, Inc.主动,不招人
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ML Bio Solutions, Inc.Virginia Commonwealth University完全的
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Centre Hospitalier Universitaire de Saint EtienneÖrebro University, Sweden; Association Française contre les Myopathies (AFM), Paris完全的
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Columbia UniversityNational Eye Institute (NEI); Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts; Universität...招聘中
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Virginia Commonwealth University招聘中
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University of OsloOslo University Hospital; Vikersund Rehabilitation Center完全的
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Expansion Therapeutics, Inc.完全的
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University of BernUniversity Hospital Inselspital, Berne; University of Lausanne Hospitals; University Children's... 和其他合作者招聘中
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Radboud University Medical Center招聘中
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University Hospital, CaenUniversity Hospital, Rouen; Centre Hospitalier Universitaire, Amiens; University Hospital, Brest; Rennes University Hospital 和其他合作者终止
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Sarepta Therapeutics, Inc.主动,不招人
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Cure CMD完全的
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta University; University... 和其他合作者招聘中
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Sarepta Therapeutics, Inc.招聘中肢带型肌营养不良美国, 巴西, 比利时, 加拿大, 德国, 意大利, 西班牙, 瑞典, 火鸡, 英国
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Sarepta Therapeutics, Inc.Nationwide Children's Hospital完全的
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Assistance Publique - Hôpitaux de ParisRecherche Clinique Paris Descartes Necker Cochin Sainte Anne; AFM-Téléthon (Funding)招聘中
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Istituto Superiore di SanitàFondazione G.B. Bietti, IRCCS; Ospedale Pediatrico Bambin Gesù招聘中
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IRCCS San Camillo, Venezia, Italy完全的强直性营养不良 1 型 (DM1)
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Swiss Federal Institute of Technology完全的
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Ohio State UniversityGilead Sciences完全的
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of Iowa主动,不招人
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Pitié-Salpêtrière Hospital招聘中
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Cure CMD招聘中Emery-Dreifuss 肌营养不良症 | 先天性肌无力综合症 | 肢带型肌营养不良症 | ITGA7(整合素 Alpha-7)缺乏症导致的先天性肌营养不良症 | Α-Dystroglycanopathy(先天性肌肉萎缩症和 Dystroglycan 异常糖基化伴有严重癫痫) | Α-肌营养不良症(由 TRAPPC11 突变引起的先天性肌营养不良伴脂肪肝和婴儿期白内障) | Α-Dystroglycanopathy(先天性肌营养不良症伴 Dystroglycan 低糖基化) | Α-肌营养不良症(先天性肌营养不良伴肌营养不良和癫痫) | Alpha-Dystroglycanopathy(Dystroglycanopathy... 及其他条件美国
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Astellas Institute for Regenerative Medicine完全的