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선천성 이적혈구형성빈혈 1형에 대한 임상 시험
총 6268 건
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Jason Robert GotlibCelgene Corporation종료됨백혈병 | 빈혈증 | 골수이형성 증후군(MDS) | 급성 골수성 백혈병(AML)미국
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Agios Pharmaceuticals, Inc.모병소아 피루브산 키나제 결핍 | 소아 용혈성 빈혈미국, 스페인, 독일, 네덜란드, 캐나다, 프랑스, 이스라엘, 스위스, 이탈리아
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Elizabeth Yang, MD, PhDUniversity of California, San Francisco; Global Blood Therapeutics; Pediatrix완전한
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health (NIH)완전한
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National Heart, Lung, and Blood Institute (NHLBI)완전한
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Children's Hospital Medical Center, Cincinnati완전한
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Duke UniversityNational Institutes of Health (NIH)완전한
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Assistance Publique - Hôpitaux de Paris완전한
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National Center for Research Resources (NCRR)Shirley Ryan AbilityLab완전한겸상 적혈구 빈혈
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Newark Beth Israel Medical Center완전한
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Novartis Pharmaceuticals완전한겸상 적혈구 빈혈칠면조, 미국, 독일, 캐나다, 영국, 이스라엘, 남아프리카
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)완전한
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National Heart, Lung, and Blood Institute (NHLBI)완전한
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St. Jude Children's Research HospitalThrasher Research Fund종료됨
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); St. Jude Children's Research Hospital; Tropical Medicine Research Institute 그리고 다른 협력자들종료됨
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Al-Neelain UniversityMilitary hospital; Ministry of Higher Education and Scientific Research, Republic of Sudan완전한
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet Association모병철분 대사 장애 | 겸상 적혈구 질환 | 지중해빈혈 | 용혈성; 빈혈, 유전성, 효소 장애로 인한 | 막 결함으로 인한 빈혈 | CDA | 철적구성 빈혈 | 체질적 재생 불량성 빈혈 | 유전성 빈혈스페인
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Tennessee; Assisi Foundation완전한
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Hillhurst Biopharmaceuticals, Inc.National Heart, Lung, and Blood Institute (NHLBI)완전한
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University of California, San Francisco완전한겸상 적혈구 질환 | 혈색소병증 | 지중해빈혈 | 혈액 악성종양 | 면역결핍 | Fanconi의 빈혈 | 비악성 질환 | 신진대사의 유전적 선천적 오류미국
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The University of Hong Kong완전한Homozygous αº-thalassemia | Hb Bart's Disease중국
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Fenwal, Inc.Children's Hospital of Philadelphia; Washington University School of Medicine; University... 그리고 다른 협력자들완전한
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National Institutes of Health Clinical Center (CC)완전한
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Wake Forest University Health SciencesNational Heart, Lung, and Blood Institute (NHLBI); Wake Forest University빼는
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Dana-Farber Cancer InstituteJohns Hopkins University; Baylor College of Medicine; Washington University School of Medicine 그리고 다른 협력자들완전한
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UCSF Benioff Children's Hospital OaklandNational Heart, Lung, and Blood Institute (NHLBI)완전한
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National Heart, Lung, and Blood Institute (NHLBI)완전한혈액 질환 | 빈혈, 낫적혈구 | 혈색소병증
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University of North Carolina완전한
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Children's Mercy Hospital Kansas CityEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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Tel-Aviv Sourasky Medical Center알려지지 않은