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Clinical Trials on Genetiske sykdommer, X-linked in United States
Totalt 7927 resultater
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Janssen Research & Development, LLCJanssen Research & Development, LLCAktiv, ikke rekrutterendeGenterapiforsøk for behandling av X-bundet retinitis Pigmentosa assosiert med varianter i RPGR-genetX-Linked Retinitis PigmentosaBelgia, Canada, Forente stater, Israel, Storbritannia, Spania, Danmark, Frankrike, Italia, Nederland, Sveits
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ShireFullførtHunters syndrom | Mukopolysakkaridose (MPS)Forente stater, Argentina, Mexico, Spania, Storbritannia
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Denali Therapeutics Inc.RekrutteringMukopolysakkaridose IIForente stater, Spania, Storbritannia, Tsjekkia, Frankrike, Canada, Italia, Belgia, Nederland, Tyskland, Argentina, Sverige, Tyrkia, Colombia, Brasil
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University of California, San DiegoBioMarin PharmaceuticalTilbaketrukketAtferdsmanifestasjoner av Lesch-Nyhans sykdomForente stater
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REGENXBIO Inc.Aktiv, ikke rekrutterendeMukopolysakkaridose type II (MPS II)Forente stater, Brasil
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REGENXBIO Inc.Aktiv, ikke rekrutterendeMukopolysakkaridose type II (MPS II)Forente stater, Canada
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ShireFullførtHunters syndromStorbritannia, Forente stater, Brasil
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston Children's Hospital og andre samarbeidspartnereFullførtPrader-Willi syndrom | Rett syndrom | Angelman syndrom | SøvnproblemerForente stater
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Cooperative International Neuromuscular Research...FullførtMuskeldystrofi, DuchenneForente stater
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasFullførtX-Linked Retinitis PigmentosaStorbritannia, Forente stater
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Baxalta now part of ShireFullført
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Nationwide Children's HospitalFullført
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Emalex Biosciences Inc.Psyadon PharmaAvsluttetLesch-Nyhan sykdom | Selvskadende oppførselSpania, Forente stater
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National Institute of Neurological Disorders and...FullførtMotor Neuron sykdom | Spinal og bulbar muskelatrofi (SBMA)Forente stater
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Sangamo TherapeuticsAvsluttet
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Kevin FlaniganMuscular Dystrophy AssociationAvsluttet
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Red Nucleus Enterprise Solutions, LLCRekruttering
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Virginia Commonwealth UniversityNorthwestern University; University of RochesterRekrutteringDuchenne muskeldystrofiForente stater
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University of FloridaRekruttering
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Phrixus Pharmaceuticals, Inc.Charley's FundAvsluttet
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Children's Hospital Medical Center, CincinnatiIpsen; Charley's FundFullførtDuchenne muskeldystrofiForente stater
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Ann & Robert H Lurie Children's Hospital of ChicagoFullført
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Kevin FlaniganTilbaketrukketDuchenne muskeldystrofiForente stater
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Alan Neuromedical Technologies, LLCFullført
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Cooperative International Neuromuscular Research...United States Department of DefenseAvsluttet
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Lundquist Institute for Biomedical Innovation at...FullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mukopolysakkaridose type VIForente stater
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CSL BehringRekruttering
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TakedaTakeda Development Center Americas, Inc.RekrutteringHunters syndrom | Mukopolysakkaridose (MPS)Forente stater
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PTC TherapeuticsFullførtDuchenne muskeldystrofiForente stater
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Cedars-Sinai Medical CenterFullførtBecker muskeldystrofiForente stater
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Cedars-Sinai Medical CenterAvsluttet
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyFullført
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Cedars-Sinai Medical CenterFullført
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationFullført
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National Human Genome Research Institute (NHGRI)Fullført
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Masonic Cancer Center, University of MinnesotaTilbaketrukket
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)AvsluttetAdrenoleukodystrofi | AdrenomyeloneuropatiForente stater
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Cooperative International Neuromuscular Research...FullførtMuskeldystrofi, DuchenneForente stater
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Har ikke rekruttert ennå
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...Rekruttering
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Massachusetts General HospitalBoston Children's HospitalRekruttering
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University of PittsburghRekrutteringDuchenne muskeldystrofiForente stater
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsFullførtDuchenne muskeldystrofiForente stater
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Sarepta Therapeutics, Inc.FullførtDuchenne muskeldystrofiForente stater
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterAktiv, ikke rekrutterende
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Craig McDonald, MDCardero Therapeutics, Inc.Fullført
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University of FloridaEngage Health Inc.Fullført
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University of FloridaUnited States Department of DefenseFullførtDuchenne muskeldystrofiForente stater
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...FullførtDuchenne muskeldystrofiForente stater
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Boston Children's HospitalBeth Israel Deaconess Medical CenterFullførtDuchenne muskeldystrofiForente stater