白内障および知的障害を伴う先天性筋ジストロフィー (MDCCAID)の臨床試験
合計757件
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University Hospital, Toulouse完了
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University Hospital, ToulouseEuropean Society for Paediatric Endocrinology完了
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Zafgen, Inc.終了しました
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Karolinska University HospitalNovo Nordisk A/S完了
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Samsung Medical Center完了
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Massachusetts General HospitalPatient-Centered Outcomes Research Institute完了
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Hugo W. Moser Research Institute at Kennedy Krieger...募集
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OPKO Health, Inc.Elan Pharmaceuticals完了
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Erasmus Medical CenterFoundation for Prader-Willi Research; Prader-Willi Fondsまだ募集していません
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The Hospital for Sick ChildrenUniversity of Western Ontario, Canada; Holland Bloorview Kids Rehabilitation Hospital募集
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Montefiore Medical CenterJazz Pharmaceuticals; Foundation for Prader-Willi Research積極的、募集していない
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Harmony Biosciences, LLC積極的、募集していない
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Radius Pharmaceuticals, Inc.Benuvia Therapeutics Inc.終了しました
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University Hospital, Toulouse完了
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Assistance Publique - Hôpitaux de Paris終了しました
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Duke UniversityNovartis; National Institutes of Health (NIH); National Center for Research Resources (NCRR)終了しました
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Children's Hospital Medical Center, Cincinnati募集
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Johns Hopkins UniversityCornelia de Lange Syndrome Foundationまだ募集していません
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Esoterix Genetic Laboratories, LLCわからない
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University Hospital, Toulouse募集
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Gedeon Richter Plc.完了
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University of Kansas Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)完了
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BioCeryxUniversity of British Columbia; University College London Hospitals; Brugmann University Hospital と他の協力者わからない
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University of FloridaNational Institutes of Health (NIH)完了