先天性アミノ酸代謝異常症の臨床試験
合計44132件
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University of Southern CaliforniaNational PKU Alliance積極的、募集していない
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University of Missouri-ColumbiaBioMarin Pharmaceutical招待による登録
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APR Applied Pharma Research s.a.終了しました
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University Hospital Inselspital, BerneUniversity of Zurich完了
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University Hospitals Cleveland Medical CenterBioMarin Pharmaceutical完了
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The University of Texas Medical Branch, Galveston終了しました
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Universidade do PortoBioMarin Pharmaceutical; Centro Hospitalar do Porto完了
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University of British ColumbiaVitaflo International, Ltdわからない
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BioMarin Pharmaceutical完了
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University of Wisconsin, MadisonBoston Children's Hospital完了
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Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science Institute完了
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Children's National Research InstituteGeorgetown University引きこもった
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Merck KGaA, Darmstadt, GermanySmerud Medical Research International AS; Merck Serono Norway完了
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The Kennedy Institute-National Eye ClinicSygekassernes Helsefond完了
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)引きこもった先天性尿素サイクル異常症 | 先天性代謝異常症 | プロピオン酸血症 | メチルマロン酸血症 | カルバミルリン酸合成酵素欠損症
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Horizon Pharma Ireland, Ltd., Dublin Ireland完了
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Horizon Pharma Ireland, Ltd., Dublin Ireland完了
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University of Novi Sad, Faculty of Sport and Physical...完了
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Baylor College of Medicine完了
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Horizon Pharma Ireland, Ltd., Dublin Ireland完了
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National Center for Research Resources (NCRR)Baylor College of Medicineわからない
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University Hospital, Clermont-Ferrandわからない
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Horizon Pharma Ireland, Ltd., Dublin Ireland完了
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare...終了しました
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Aeglea Biotherapeutics完了
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University of TorontoIovate Health Sciences International Inc完了
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S.LAB (SOLOWAYS)Center of New Medical Technologies募集
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Peking UniversityNational Natural Science Foundation of China; Institute of reproductive and Child Health完了
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The Hospital for Sick ChildrenBioMarin Pharmaceutical完了
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Baylor Research InstituteNational Institutes of Health (NIH)完了
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Center for Health, Exercise and Sport Sciences,...完了
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BioMarin Pharmaceutical募集
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PTC Therapeutics完了
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Homology Medicines, Inc終了しました