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Clinical Trials on 유전 질환, X-연관 in United States
총 7962 건
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Eunice Kennedy Shriver National Institute of Child...알려지지 않은
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Indiana UniversityIndiana Clinical and Translational Sciences Institute완전한
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Stanford UniversityNational Institute of Mental Health (NIMH); Autism Speaks완전한
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NightstaRx Ltd, a Biogen Company초대로 등록맥락막결절증 | X-연관 색소성 망막염미국, 영국, 네덜란드, 독일, 프랑스, 브라질, 캐나다, 덴마크, 핀란드
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National Institute of Allergy and Infectious Diseases...모병
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children's Hospital; Vanderbilt University Medical Center 그리고 다른 협력자들모병
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); National Institute of Neurological Disorders and Stroke (NINDS) 그리고 다른 협력자들완전한
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)완전한
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Boston Children's HospitalInternational Rett Syndrome Foundation완전한
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Boston Children's HospitalAutism Speaks; International Rett Syndrome Foundation완전한
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Great Ormond Street Hospital for Children NHS Foundation...모병
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National Human Genome Research Institute (NHGRI)완전한
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.org모병
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome Foundation완전한
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Novartis Pharmaceuticals완전한
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama at Birmingham 그리고 다른 협력자들모병
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research Trust알려지지 않은
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Edimer Pharmaceuticals완전한저발한성 외배엽 이형성증 | X-연관 저발한성 외배엽 이형성증미국
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Edimer PharmaceuticalsNational Foundation of Ectodermal Dysplasia완전한
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.org완전한
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Rett Syndrome Research TrustVanderbilt University Medical Center완전한
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Novartis Pharmaceuticals종료됨취약 X 증후군독일, 미국, 스위스, 호주, 캐나다, 덴마크, 프랑스, 이탈리아, 영국, 스페인
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Nova Mentis Life Science CorpFourthWall Testing모병
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Eunice Kennedy Shriver National Institute of Child...모병
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Viking Therapeutics, Inc.모병X-연관 부신백질이영양증(X-ALD)의 부신척수신경병증 형태(AMN)미국, 프랑스, 독일, 이탈리아, 영국