- ICH GCP
- 미국 임상 시험 레지스트리
- Search trials
미토콘드리아 유전 장애에 대한 임상 시험
총 152060 건
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Larimar Therapeutics, Inc.Clinilabs, Inc.완전한
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLC완전한
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University of South FloridaFriedreich's Ataxia Research Alliance; Edison Pharmaceuticals Inc완전한
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University of South Florida알려지지 않은
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National Institute of Neurological Disorders and...완전한
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical Inc더 이상 사용할 수 없음바르트 증후군 | 미토콘드리아 삼중기능 단백질 결핍 | 초장쇄 acylCoA 탈수소효소(VLCAD) 결핍증 | 카르니틴 팔미토일전이효소 결핍(CPT1, CPT2) | 장쇄 하이드록시아실-CoA 탈수소효소 결핍증 | 글리코겐 저장 장애 | 피루브산 카르복실라제 결핍증 | ACYL-CoA DEHYDROGENASE FAMILY, MEMBER 9, DEFICIENCY of미국
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Sanquin-LUMC J.J van Rood Center for Clinical Transfusion...Leiden University Medical Center완전한
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Massachusetts General HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)알려지지 않은
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)모병
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases Clinical...모병
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Byron LamNational Eye Institute (NEI)모집하지 않고 적극적으로
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University of PittsburghFriedreich's Ataxia Research Alliance완전한
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Santhera Pharmaceuticals완전한프라이드라이히 운동실조증독일, 네덜란드, 프랑스, 오스트리아, 벨기에
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Murdoch Childrens Research InstituteFriedreich's Ataxia Research Alliance완전한
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Chun Pan알려지지 않은
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Jirair Krikor BedoyanUltragenyx Pharmaceutical Inc모병
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Saol Therapeutics Inc 그리고 다른 협력자들모집하지 않고 적극적으로
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Fondazione Telethon완전한
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Nantes University HospitalUniversity Hospital, Angers; University Hospital, Brest; Rennes University Hospital; University...완전한
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of Rochester모병
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Santhera Pharmaceuticals더 이상 사용할 수 없음
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University of MinnesotaFriedreich's Ataxia Research Alliance; Bob Allison Ataxia Research Center완전한
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Stealth BioTherapeutics Inc.완전한
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Adverum Biotechnologies, Inc.Adverum Biotechnologies SAS, a wholly owned subsidiary of Adverum Biotechnologies, Inc.완전한
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The University of Texas Health Science Center at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)완전한
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Oregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Oregon State...종료됨
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Sanquin-LUMC J.J van Rood Center for Clinical Transfusion...Leiden University Medical Center완전한
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Medical University of Graz완전한
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Steen Hvitfeldt Poulsen완전한트랜스티레틴 아밀로이드 심장병증 | 미토콘드리아 병리학덴마크
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Sanquin-LUMC J.J van Rood Center for Clinical Transfusion...Erasmus Medical Center; Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA); Leiden University Medical Center종료됨
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M.D. Anderson Cancer Center모병
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Eunice Kennedy Shriver National Institute of Child...모병
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Institut National de la Santé Et de la Recherche...Commissariat A L'energie Atomique; Imagine Institute완전한