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모노카르복실레이트 수송체 8 결핍에 대한 임상 시험
총 178 건
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Dana-Farber Cancer Institute알려지지 않은
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Inozyme Pharma아직 모집하지 않음유아기의 일반화 동맥 석회화 | 상염색체 열성 저인산혈증 구루병 | 엑토뉴클레오타이드 파이로포스파타아제/포스포디에스테라아제1 결핍 | ATP 결합 카세트 서브패밀리 C 구성원 6 결핍
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Assistance Publique - Hôpitaux de ParisEuroFancolen완전한
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)완전한
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Shenzhen Geno-Immune Medical Institute알려지지 않은
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Medical College of WisconsinMemorial Sloan Kettering Cancer Center완전한
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National Heart, Lung, and Blood Institute (NHLBI)완전한
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical Center,...완전한
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)완전한
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products Development완전한
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University of Minnesota알려지지 않은
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Masonic Cancer Center, University of Minnesota완전한
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERER완전한
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, Cincinnati완전한
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of Texas, Southwestern...종료됨
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University of Minnesota완전한
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy, Baylor College...종료됨
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Rocket Pharmaceuticals Inc.알려지지 않은
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Children's Hospital Medical Center, CincinnatiAmgen완전한
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Rocket Pharmaceuticals Inc.초대로 등록
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National Center for Research Resources (NCRR)University of California, San Diego완전한판코니 증후군 | 시스틴증
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de la Fundación... 그리고 다른 협력자들완전한
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Cystinosis Research Foundation알려지지 않은
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Assistance Publique - Hôpitaux de Paris아직 모집하지 않음
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Porteus, Matthew, MD모병
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma Limited종료됨
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)완전한
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NYU Langone HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)완전한
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)완전한상세불명 소아기 고형 종양, 프로토콜 특정 | 상세불명의 성인 고형 종양, 프로토콜 특정 | 판코니빈혈미국
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National Heart, Lung, and Blood Institute (NHLBI)완전한
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Universitaire Ziekenhuizen KU LeuvenKU Leuven알려지지 않은
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Rocket Pharmaceuticals Inc.모집하지 않고 적극적으로
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Boston Children's Hospital종료됨
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institutes... 그리고 다른 협력자들모병
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Westfälische Wilhelms-Universität MünsterICON plc알려지지 않은
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National Human Genome Research Institute (NHGRI)완전한유아기의 일반화 동맥 석회화 | 상염색체 열성 저인산혈증 구루병 Type2미국
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor Consortium종료됨