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선천성 근이영양증 유형 1A에 대한 임상 시험
총 7628 건
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Wake Forest University Health SciencesMuscular Dystrophy Association완전한
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Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell Therapy완전한
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Monica Levy Andersen완전한Other Diseases or Conditions브라질
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PTC TherapeuticsMuscular Dystrophy Association완전한
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Ionis Pharmaceuticals, Inc.완전한
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Newcastle-upon-Tyne Hospitals NHS Trust완전한
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University of Florida; Stanford... 그리고 다른 협력자들완전한
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Stanford University알려지지 않은
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed Incorporated완전한
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PTC TherapeuticsGenzyme, a Sanofi Company종료됨
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University Hospital, Toulouse알려지지 않은
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Oslo University HospitalUniversity Hospital of North Norway; The Research Council of Norway완전한
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of Technology완전한
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University of CalgaryMuscular Dystrophy Canada초대로 등록
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AbiliTech Medical Inc.Richard M. Schulze Family Foundation모병
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Institut de Myologie, France초대로 등록
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Insmed IncorporatedMuscular Dystrophy Association완전한
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Mayo ClinicNational Eye Institute (NEI)완전한망막질환 | 최고의 Vitelliform 황반 이영양증 | Bestrophinopathy | 성인 발병 Vitelliform 황반 이영양증 | 상염색체 우성 유리체망막맥락막병증미국
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Hacettepe University완전한
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L.V. Prasad Eye InstituteAllergan모병
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Suzuka HospitalNagoya University알려지지 않은
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Nationwide Children's HospitalParent Project Muscular Dystrophy완전한
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Holland Bloorview Kids Rehabilitation HospitalChildren's Hospital of Eastern Ontario완전한
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PTC Therapeutics완전한신경계 질환 | 유전병, 선천적 | 유전 질환, X-연관 | 근육질병 | 신경근 질환 | 근이영양증 | 근육 장애, 위축 | 근이영양증, Duchenne | 근골격계 질환미국, 대만, 인도, 대한민국, 태국, 호주, 브라질, 불가리아, 캐나다, 중국, 홍콩, 말레이시아, 멕시코, 폴란드, 푸에르토 리코, 러시아 연방, 칠면조, 일본
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Istituto Auxologico Italiano완전한골다공증 | 뒤시엔 근이영양증
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), Paris완전한
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Centre Hospitalier Universitaire de Nice완전한
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National Eye Institute (NEI)National Cancer Institute (NCI)모병
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of Munich; University...완전한
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Peking Union Medical College HospitalNational Natural Science Foundation of China; Cancer Institute and Hospital, Chinese Academy...모병
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Hacettepe University완전한
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Hacettepe University완전한
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Jett Foundation, Inc.Pfizer; Hoffmann-La Roche; Italfarmaco; Nationwide Children's Hospital; Capricor Inc.; Santhera... 그리고 다른 협력자들완전한