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Clinical Trials on Pyruvatmetabolisme, medfødte feil in United States
Totalt 2366 resultater
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AlexionRekruttering
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Brigham and Women's HospitalAktiv, ikke rekrutterendeASCVD | Hyperlipemi, blandetForente stater
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldAktiv, ikke rekrutterende
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Dr. Schär AG / SPAFullførtFenylketonuri | Medfødte stoffskiftefeil | Metabolsk sykdom | PKUStorbritannia
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Lumos DiagnosticsAptatek BiosciencesRekruttering
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Emory UniversityBioMarin PharmaceuticalRekrutteringFenylketonuriForente stater
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Rubius TherapeuticsAvsluttet
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Boston Children's HospitalBrigham and Women's HospitalFullført
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalFullførtFenylketonuriForente stater
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University of Missouri-ColumbiaBioMarin PharmaceuticalFullførtFenylketonuriForente stater
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Emory UniversityAtlanta Clinical and Translational Science InstituteFullført
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The University of Texas Health Science Center,...BioMarin PharmaceuticalAvsluttetFenylketonuri | HyperfenylalaninemiForente stater
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalFullførtFenylketonuriForente stater
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The University of Texas Health Science Center,...BioMarin PharmaceuticalFullført
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Massachusetts General HospitalRekruttering
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Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationFullførtHomozygot familiær hyperkolesterolemiForente stater
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PTC TherapeuticsRekrutteringFenylketonuriForente stater
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Boston Children's HospitalBioMarin PharmaceuticalFullførtFenylketonuriForente stater
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University of NebraskaFullført
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University Hospitals Cleveland Medical CenterBioMarin PharmaceuticalFullført
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The University of Texas Medical Branch, GalvestonAvsluttet
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Boston Children's HospitalBioMarin PharmaceuticalFullført
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Oregon Health and Science UniversityAvsluttet
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UniQure Biopharma B.V.Chiesi Farmaceutici S.p.A.Tilbaketrukket
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Medical Research Laboratories InternationalAvsluttetFamiliær hyperkolesterolemiNederland, Forente stater, Norge
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Vanderbilt University Medical CenterRekrutteringPseudohypoparathyroidisme Type 1a | Albright arvelig osteodystrofi | PseudohypoparathyroidismeForente stater
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Ashley ShoemakerPåmelding etter invitasjonPseudohypoparathyroidisme Type 1a | Albright arvelig osteodystrofi | PseudohypoparathyroidismeForente stater
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Vanderbilt University Medical CenterMassachusetts General HospitalFullførtPseudohypoparathyroidisme Type 1a | Albright arvelig osteodystrofiForente stater
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University of California, San DiegoFullførtAlkaptonuriaForente stater
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Sheffield Teaching Hospitals NHS Foundation TrustFullført
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Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin PharmaceuticalFullført
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Shoji YanoBioMarin PharmaceuticalFullførtFenylketonuriForente stater
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National Human Genome Research Institute (NHGRI)RekrutteringPropionsyreacidemi | Metabolsk sykdom | Organisk acidemiForente stater
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Vitaflo International, LtdFullført
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Eunice Kennedy Shriver National Institute of Child...Fullført
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Vitaflo International, LtdOregon Health and Science UniversityFullført
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Children's Hospital Medical Center, CincinnatiBioMarin PharmaceuticalFullført
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University of MiamiFullførtFenylketonuriForente stater
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Children's Hospital of PhiladelphiaFullført
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University of Southern CaliforniaNational PKU AllianceAktiv, ikke rekrutterendeFenylketonuriForente stater
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Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science InstituteFullført
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National Human Genome Research Institute (NHGRI)Rekruttering
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TakedaAvsluttetHyperkolesterolemiFrankrike, Storbritannia, Forente stater, Israel, Polen, Canada
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Alexion Pharmaceuticals, Inc.RekrutteringHypofosfatasiAustralia, Forente stater, Japan, Tyskland, Tyrkia, Italia, India, Frankrike, Storbritannia, Argentina, Canada
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustFullført
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRekrutteringFamiliær hyperkolesterolemi | Genetisk sykdom | Kolesterol, forhøyetForente stater
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National Heart, Lung, and Blood Institute (NHLBI)Fullført
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University of South FloridaNational Institutes of Health (NIH)FullførtUreasyklusforstyrrelserForente stater