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Kliniske forsøg med AMC-Arthrogryposis Multiplex Congenita
I alt 1380 resultater
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Ovid Therapeutics Inc.Afsluttet
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Radboud University Medical CenterIpsenAfsluttetLeversygdomme | Polycystisk nyre, autosomal dominant | Hepatomegali | Polycystisk leversygdomHolland, Belgien
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Centre Hospitalier Sud FrancilienIkke rekrutterer endnu
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University of Kansas Medical CenterIkke rekrutterer endnuFedme | Alzheimers sygdom | Downs syndromForenede Stater
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Imagine InstituteRWTH Aachen University; Ruhr University of Bochum; Medical University of...RekrutteringEpilepsi | Tuberøs skleroseFrankrig
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University Hospital, Strasbourg, FranceRekruttering
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Lisa Guay WoodfordRekruttering
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National Institute of Neurological Disorders and...Aktiv, ikke rekrutterendeHemangioblastom | Hippel Lindaus sygdomForenede Stater
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LuMind IDSC FoundationAlzheimer's Disease Cooperative Study (ADCS)Aktiv, ikke rekrutterendeAlzheimers sygdom i Downs syndromForenede Stater
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Brigham and Women's HospitalChildren's Hospital of Philadelphia; University of Michigan; University of... og andre samarbejdspartnereAfsluttetSøvnforstyrret vejrtrækning | Downs syndromForenede Stater
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Istanbul Medipol University HospitalUkendtKarpaltunnelsyndrom | Palmaris Longus muskel, fravær af | EMG syndromKalkun
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University of California, Los AngelesEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereUkendt
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National Human Genome Research Institute (NHGRI)AfsluttetHjernelidelser | Holoprosencefali | HPE | Forsinkede udviklingsforstyrrelserForenede Stater
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University Hospital, MontpellierUkendtTuberøs sklerosekompleksFrankrig
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Duke UniversityFoundation for Prader-Willi ResearchAfsluttetFedme hos børn | Prader Willi Syndrom | Syndromisk fedmeForenede Stater, Canada
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRekrutteringFanconi Anæmi | Myelodysplastisk syndrom (MDS) | Akut myelogen leukæmi (AML) | Alvorlig marvsvigtForenede Stater
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Bellicum PharmaceuticalsAfsluttetLymfom, Non-Hodgkin | Akut lymfatisk leukæmi | Primær immundefekt | Anæmi, seglcelle | Hæmoglobinopatier | Fanconi Anæmi | Anæmi, aplastisk | Myelodysplastisk syndrom | Thalassæmi | Cytopeni | Diamond Blackfan Anæmi | Osteopetrose | Leukæmi, akut myeloid (AML), barnDet Forenede Kongerige, Italien
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National Cancer Institute (NCI)RekrutteringNeurofibromatose 1 | Noonans syndrom | Legius syndrom | Kardiofaciokutant syndrom | Costello syndromForenede Stater
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Natera, Inc.AfsluttetTrisomi 21 | Trisomi 18 | Trisomi 13 | Kønskromosomafvigelser | MikrodeletionssyndromerForenede Stater, Spanien, Taiwan
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AmgenAfsluttetAkut myeloid leukæmi | Myelomatose | AML | Myelodysplastisk syndrom | MDS | Non-Hodgkins lymfom | NHLForenede Stater, Australien, Italien, Frankrig, Grækenland, Japan
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Boston Children's HospitalNational Eye Institute (NEI); Howard Hughes Medical InstituteRekrutteringØjenmotilitetsforstyrrelser | Facial parese | Synkinesis | Sjette nerve parese | Mobius syndrom | Medfødt fibrose af ekstraokulære muskler | Duane Retraction Syndrome | Duane Radial Ray Syndrom | Brunt syndrom | Marcus Gunns syndrom | Strabismus medfødt | Horisontal Gaze Parese | Horisontal blikparese med progressiv... og andre forholdForenede Stater
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ACADIA Pharmaceuticals Inc.RekrutteringHyperfagi i Prader-Willi syndromForenede Stater, Canada, Det Forenede Kongerige
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Universitair Ziekenhuis BrusselIkke rekrutterer endnu
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University Hospital, BrestIkke rekrutterer endnu
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University Medical Center GroningenRadboud University Medical CenterRekrutteringAutosomal dominant polycystisk nyre | Polycystisk leversygdomHolland
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University Medical Center GroningenIkke rekrutterer endnuADPKDHolland, Det Forenede Kongerige, Belgien, Tyskland, Frankrig, Spanien
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Erasmus Medical CenterRekruttering
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Katarzyna KotulskaRekruttering
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University of Colorado, DenverRekrutteringAlzheimers sygdom | Downs syndrom | Mild kognitiv svækkelseForenede Stater
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ACADIA Pharmaceuticals Inc.Tilmelding efter invitationHyperfagi i Prader-Willi syndromForenede Stater
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University Hospitals Bristol and Weston NHS Foundation...University College, London; The Tuberous Sclerosis AssociationAktiv, ikke rekrutterendeTuberøs sklerosekompleksDet Forenede Kongerige
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University of Alabama at BirminghamUltragenyx Pharmaceutical IncAfsluttetEpidermalt Nevus SyndromForenede Stater
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University Hospital ErlangenPervormance GmbHAfsluttetX-forbundet hypohidrotisk ektodermal dysplasi | Træningsinduceret stigning i kropstemperaturenTyskland
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University Hospital, Strasbourg, FranceAfsluttet
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University of California, Los AngelesBoston Children's HospitalAfsluttetTuberøs sklerosekompleksForenede Stater
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University of PennsylvaniaH. Lundbeck A/SAfsluttetKomplekse partielle anfaldForenede Stater
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Children's Hospital Medical Center, CincinnatiMassachusetts General Hospital; The University of Texas Health Science... og andre samarbejdspartnereAfsluttetTuberøs sklerosekompleksForenede Stater
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Michael RafiiJanssen Research & Development, LLCAfsluttet
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Centre Hospitalier Universitaire de Saint EtienneMinistry of Health, FranceAfsluttet
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Children's Treatment NetworkMcMaster UniversityAfsluttetCerebral Parese | Hjerneskade | Autisme | Downs syndromCanada
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National Institute on Aging (NIA)UkendtDowns syndrom | Alzheimers sygdomForenede Stater
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University of Colorado, DenverAfsluttetMarfan syndrom | Turners syndrom | Loeys-Dietz syndrom | Thorax aortaaneurisme og dissektionssyndromer | Ehlers-Danlos Type IV syndromForenede Stater
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Cairo UniversityAfsluttetAzoospermi Anogenital Afstand AMHEgypten
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Tragara Pharmaceuticals, Inc.AfsluttetMyelomatose | AML | Blast krise | MDS | ALLEForenede Stater
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University of California, Los AngelesRekrutteringTuberøs skleroseForenede Stater
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University of RochesterUnited States Department of DefenseRekruttering
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Corporacion Parc TauliInstituto de Salud Carlos IIIRekrutteringSøvnforstyrrelse | Hyperfagi | AdfærdsforstyrrelserSpanien
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Children's Hospital Medical Center, CincinnatiAfsluttetEpilepsi | Tuberøs sklerosekompleksForenede Stater
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Rhythm Pharmaceuticals, Inc.AfsluttetBardet-Biedl syndrom | POMC-mangel Fedme | PCSK1 Mangel Fedme | LEPR-mangel FedmeForenede Stater, Australien, Spanien, Det Forenede Kongerige
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Jazz PharmaceuticalsAfsluttetAnfald | Tuberøs sklerosekompleksForenede Stater, Spanien, Australien, Polen, Det Forenede Kongerige, Holland