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Clinical Trials on Epidermolysis Bullosa Dystrophica in United States
I alt 671 resultater
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Beacon TherapeuticsAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater
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Stanford UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of California... og andre samarbejdspartnereAfsluttetMuskeldystrofi, DuchenneForenede Stater
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Rekruttering
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Cure CMDAfsluttetMedfødt muskeldystrofiForenede Stater
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Columbia UniversityNational Eye Institute (NEI); Centre Hospitalier National d'Ophtalmologie... og andre samarbejdspartnereRekrutteringRetinitis Pigmentosa | Bedste Vitelliform Macula DystrophyForenede Stater, Tyskland, Frankrig
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Massachusetts General HospitalRekruttering
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Nationwide Children's HospitalParent Project Muscular DystrophyRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...AfsluttetGNE myopati | Hereditary Inclusion Body Myopati (HIBM)Forenede Stater
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Cedars-Sinai Medical CenterAfsluttet
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of... og andre samarbejdspartnereAfsluttetDuchennes muskeldystrofiForenede Stater
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Wake Forest University Health SciencesAfsluttetFuchs dystrofi | Cystoid makulært ødemForenede Stater
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Cooperative International Neuromuscular Research...AfsluttetMuskeldystrofi, DuchenneForenede Stater
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PTC TherapeuticsAfsluttetDuchennes muskeldystrofiForenede Stater
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Cedars-Sinai Medical CenterAfsluttetBeckers muskeldystrofiForenede Stater
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Cedars-Sinai Medical CenterAfsluttetMuskeldystrofiForenede Stater
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyAfsluttet
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Cedars-Sinai Medical CenterAfsluttetDuchennes muskeldystrofiForenede Stater
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationAfsluttet
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National Center for Research Resources (NCRR)Children's National Research InstituteAfsluttet
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Spark TherapeuticsAktiv, ikke rekrutterendeBekræftet biallel RPE65 mutationsassocieret nethindedystrofiForenede Stater
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Beacon TherapeuticsTilmelding efter invitationX-Linked Retinitis PigmentosaForenede Stater
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Nanoscope Therapeutics Inc.AfsluttetRetinitis Pigmentosa | NethindedystrofiForenede Stater, Puerto Rico
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MeiraGTx UK II LtdJanssen, LPAktiv, ikke rekrutterendeRetinitis PigmentosaForenede Stater, Det Forenede Kongerige, Canada
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Endogena Therapeutics, IncAktiv, ikke rekrutterendeRetinitis Pigmentosa | Retinitis Pigmentosa syndromForenede Stater
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aTyr Pharma, Inc.AfsluttetFacioscapulohumeral muskeldystrofiForenede Stater, Italien, Holland
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Benitec Biopharma, Inc.RekrutteringOculopharyngeal muskeldystrofiForenede Stater
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University of FloridaAfsluttet
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Children's National Research InstituteFoundation to Eradicate DuchenneAktiv, ikke rekrutterendeDuchennes muskeldystrofiForenede Stater
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)AfsluttetMuskeldystrofi, DuchenneForenede Stater
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Cooperative International Neuromuscular Research...Afsluttet
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University of RochesterAfsluttet
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed...Afsluttet
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Columbia UniversityLudwig-Maximilians - University of Munich; Moorfields Eye Hospital NHS... og andre samarbejdspartnereRekrutteringRetinitis Pigmentosa associeret med CNGB1-mutationerForenede Stater, Frankrig, Tyskland, Det Forenede Kongerige
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University of ChicagoRekrutteringMuskeldystrofi | Arytmi | KardiomyopatiForenede Stater
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Craig McDonald, MDCardero Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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PfizerAfsluttetDuchenne muskeldystrofi (DMD)Forenede Stater
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4D Molecular TherapeuticsAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRekrutteringBeckers muskeldystrofiForenede Stater, Italien
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Cooperative International Neuromuscular Research...Afsluttet
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Johns Hopkins UniversityNational Eye Institute (NEI); Carnegie Mellon UniversityRekrutteringRetinitis Pigmentosa | Synshandicap | Visuel proteseForenede Stater
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsAfsluttetBeckers muskeldystrofi | Sund frivilligForenede Stater
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University of FloridaU.S. Army Medical Research and Development CommandRekrutteringDuchenne muskeldystrofi (DMD)Forenede Stater
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PTC TherapeuticsAfsluttetNonsene mutation Duchenne muskeldystrofiForenede Stater
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Avidity Biosciences, Inc.Tilmelding efter invitationDuchennes muskeldystrofi | DMD | Exon 44 | DuchenneForenede Stater
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Children's Hospital Medical Center, CincinnatiAktiv, ikke rekrutterendeMuskuloskeletale abnormiteter | Duchennes muskeldystrofiForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetMeddelelse | Genetisk sygdomForenede Stater
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Ann & Robert H Lurie Children's Hospital of ChicagoChildren's National Research InstituteTrukket tilbageDuchenne muskeldystrofi (DMD)Forenede Stater
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Rare Disease Research, LLCSarepta Therapeutics, Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesIkke længere tilgængeligMedfødt muskeldystrofi på grund af Lamin A/C-mutationForenede Stater
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University of Kansas Medical CenterNational Institutes of Health (NIH)AfsluttetFacioscapulohumeral muskeldystrofiForenede Stater