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Clinical Trials on Nondystrofiske myotonier in United States
I alt 45 resultater
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Myotonic Dystrophy FoundationRekrutteringMyotonisk dystrofi | Myotonisk dystrofi 1 | Steinerts sygdom | Medfødt myotonisk dystrofi | PROMM (proksimal myotonisk myopati) | Steinerts sygdom | Dystrophia Myotonica 1 | Myotonisk dystrofi 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonisk dystrofi, medfødt | Myotonisk myopati,... og andre forholdForenede Stater
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)AfsluttetMyotoniske lidelser | Myotonia Congenita | Nondystrofiske myotonierCanada, Forenede Stater, Det Forenede Kongerige
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Ohio State UniversityGilead SciencesAfsluttetMyotonisk dystrofi 1 | Myotonia Congenita | Paramyotonia CongenitaForenede Stater
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Stanford UniversityBiogenAktiv, ikke rekrutterendeMyotonisk dystrofi 1Forenede Stater
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University College, LondonRekrutteringIkke-dystrofisk myotoniDet Forenede Kongerige
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RekrutteringMuskeldystrofi | Myotonisk dystrofi type 2 | Myotonisk dystrofi type 1 | Myotonisk dystrofi | Facioscapulohumeral muskeldystrofi | Steinerts sygdom | Medfødt myotonisk dystrofi | PROMM (proksimal myotonisk myopati) | Myotonisk muskeldystrofiForenede Stater
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Richard Barohn, MDAfsluttetIkke-dystrofisk myotoni | MyotoniForenede Stater, Canada, Italien, Det Forenede Kongerige
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National Institute of Neurological Disorders and...AfsluttetMyotonisk dystrofi Type-1 | Myotonisk dystrofi Type-2Forenede Stater
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Avidity Biosciences, Inc.AfsluttetMyotonisk dystrofi | Myotoniske lidelser | Myotonisk dystrofi type 1 (DM1) | Myotonisk dystrofi 1 | Myotonisk muskeldystrofi | DM1 | Dystrofi Myotonisk | Steinerts sygdomForenede Stater
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Expansion Therapeutics, Inc.AfsluttetMyotonisk dystrofi | Myotonisk dystrofi, type 1 (DM1)Forenede Stater
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Virginia Commonwealth UniversityRekrutteringMedfødt myotonisk dystrofi | Myotonisk dystrofi i barndommen | CDM | CHDMForenede Stater, Italien
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University of Iowa og andre samarbejdspartnereRekrutteringMyotonisk dystrofi 1Forenede Stater, Holland, Det Forenede Kongerige, New Zealand, Tyskland, Italien, Canada, Frankrig
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Avidity Biosciences, Inc.Aktiv, ikke rekrutterendeSygdomme i nervesystemet | Genetiske sygdomme, medfødte | Muskuloskeletale sygdomme | Muskelsygdomme | Neuromuskulære sygdomme | Neurodegenerative sygdomme | Muskeldystrofier | Muskellidelser, atrofisk | Heredodegenerative lidelser, nervesystem | Myotonisk dystrofi | Myotoniske lidelser | Myotonisk dystrofi 1 | DM1Forenede Stater
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PepGen IncRekrutteringMyotonisk dystrofi 1Forenede Stater, Canada
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Vertex Pharmaceuticals IncorporatedRekrutteringMyotonisk dystrofi type 1 (DM1)Det Forenede Kongerige, Canada, Australien
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Dyne TherapeuticsRekrutteringMyotonisk dystrofi type 1 (DM1)Det Forenede Kongerige, Frankrig, Holland, Italien, Tyskland, New Zealand
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Stanford UniversityUkendtMyotonisk dystrofi type 1Forenede Stater
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University of RochesterAfsluttet
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed...Afsluttet
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RekrutteringMyotonisk dystrofi type 2Forenede Stater
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... og andre samarbejdspartnereAfsluttetMyotonisk dystrofi type 1Forenede Stater
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Massachusetts General HospitalRekruttering
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute og andre samarbejdspartnereRekrutteringMedfødt myotonisk dystrofiForenede Stater, Italien, Canada
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Ionis Pharmaceuticals, Inc.AfsluttetMyotonisk dystrofi type 1Forenede Stater
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AMO Pharma LimitedRekrutteringMedfødt myotonisk dystrofiForenede Stater, Canada, Australien, New Zealand
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Harmony Biosciences, LLCAktiv, ikke rekrutterendeMyotonisk dystrofi 1 | Overdreven søvnighed i dagtimerneForenede Stater, Canada
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Insmed IncorporatedMuscular Dystrophy AssociationAfsluttet
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Newcastle-upon-Tyne Hospitals NHS TrustAfsluttetMyotonisk dystrofi type 1Det Forenede Kongerige
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University College, LondonNational Institute for Health Research, United Kingdom; Myotonic Dystrophy... og andre samarbejdspartnereRekrutteringMyotonisk dystrofi 1 | Dysfagi, OrofaryngealDet Forenede Kongerige
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AMO Pharma LimitedAfsluttetMedfødt myotonisk dystrofiForenede Stater, Canada, New Zealand, Australien, Det Forenede Kongerige
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University... og andre samarbejdspartnereAfsluttetMyotonisk dystrofi type 1Holland, Frankrig, Tyskland, Det Forenede Kongerige
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AMO Pharma LimitedAfsluttetMyotonisk dystrofi 1Det Forenede Kongerige
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Indiana University School of MedicineMuscular Dystrophy AssociationAfsluttetMuskeldystrofi | Arytmi | Pludselig hjertedødForenede Stater
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Rekruttering
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Lupin Ltd.Aktiv, ikke rekrutterendeMyotonisk dystrofiFrankrig, Tyskland, Det Forenede Kongerige
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Newcastle UniversityRekrutteringMyotonisk dystrofiDet Forenede Kongerige
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's... og andre samarbejdspartnereRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofi | Myotonisk dystrofi | Facioscapulohumeral muskeldystrofiForenede Stater
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Tilmelding efter invitationHypertrofisk kardiomyopati (HCM) | Langt QT-syndrom (LQTS) | Katekolaminerg polymorf ventrikulær takykardi (CPVT) | Arvelige hjertearytmier | Brugada syndrom (BrS) | Tidlig repolariseringssyndrom (ERS) | Arytmogen kardiomyopati (AC, ARVD/C) | Dilateret kardiomyopati (DCM) | Muskelsvind (Duchenne, Becker... og andre forholdForenede Stater
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University of Texas Southwestern Medical CenterMassachusetts General HospitalRekrutteringDystoni | Dystoni; Idiopatisk | Dystoni, Primær | Dystoni, sekundær | Dystoni, familiær | Dystoni lidelse | Dystonier, sporadisk | Dystoni; Orofacial | Dystonia Lenticularis | Dystoni, Paroxysmal | Dystoni 6 | Dystoni 5 | Dystoni 8 | Dystoni 9 | Dystoni 19 | Dystoni 10 | Dystoni 11 | Dystoni 20 | Dystoni 12 | Dystoni, Focal | Hoveddystoni | Dystoni...Forenede Stater
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University of Southern CaliforniaNational Institutes of Health (NIH); Crowley Carter Foundation; Don and Linda...Ukendt
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Washington University School of MedicineNational Institute of Neurological Disorders and Stroke (NINDS)AfsluttetSund og rask | Focal DystoniasForenede Stater
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Duke UniversityVirtual PortsTrukket tilbageLaparoskopisk ærmegatrektomi | Minimalt invasiv kirurgisk procedure | Laparoskopisk mavebånd | Laparoskopisk Roux-en-Y gastrisk bypass | Laparoskopisk fundoplication procedure | Laparoskopisk Heller Myotomi | Laparoskopisk paraesophageal brok reparation | Laparoskopisk gastrisk resektionForenede Stater
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Indiana UniversityNational Institutes of Health (NIH)RekrutteringLarynx dystoni | Adductor Spastic Dysphonia of DystoniaForenede Stater
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University of Texas Southwestern Medical CenterAfsluttetCervikal dystoni | Spasticitet, muskel | Hemifaciale Spasmer | Blefarospasme | Lemmer dystoni | Fragmenter af Torsion DystoniForenede Stater
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Sanguine BiosciencesAfsluttetDepression | Melanom | Epilepsi | Lymfom | Multipel sclerose | Nyrekræft | Livmoderhalskræft | Diabetes mellitus | Leukæmi | Brystkræft | Kroniske nyresygdomme | Kronisk obstruktiv lungesygdom | Parkinsons sygdom | Systemisk lupus erythematosus | Myelomatose | Hepatitis B | Søvnløshed | Kolorektal cancer | HIV/AIDS | Kræft i bugspytkirtlen og andre forholdForenede Stater