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Prove cliniche su Anemia diseritropoyética congénita tipo 1
Totale 7287 risultati
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Dana-Farber Cancer InstituteMerck Sharp & Dohme LLC; Boston Children's Hospital; Brigham and Women's HospitalTerminatoAnemia falciforme | Anemia falciformeStati Uniti
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Completato
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)SconosciutoAnemia falciformeStati Uniti
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IcagenCompletatoAnemia falciforme | Anemia falciformeStati Uniti
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National Institute of Diabetes and Digestive and...CompletatoAnemia falciforme | Emoglobina SC MalattiaStati Uniti
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IcagenJohnson & Johnson Pharmaceutical Research & Development, L.L.C.TerminatoAnemia falciforme | Anemia falciformeStati Uniti
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Ann & Robert H Lurie Children's Hospital of ChicagoMayo Clinic; National Institute of Diabetes and Digestive and Kidney Diseases...CompletatoIperossaluria primaria di tipo 1
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University of California, San FranciscoCompletatoAnemia falciforme | Emoglobinopatie | Talassemia | Neoplasie ematologiche | Immunodeficienze | Anemia di Fanconi | Malattie non maligne | Errori genetici congeniti del metabolismoStati Uniti
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University of NebraskaReclutamentoCrisi vaso-occlusiva | Crisi di anemia falciformeStati Uniti
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Lundquist Institute for Biomedical Innovation at...Emmaus Medical, Inc.Terminato
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Emmaus Medical, Inc.FDA Office of Orphan Products DevelopmentCompletatoAnemia falciforme | TalassemiaStati Uniti
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Mansoura UniversityCompletatoRetrognatismo mandibolare | Classe II Divisione 1 MalocclusioneEgitto
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CANbridge (Suzhou) Bio-pharma Co., Ltd.ReclutamentoMalattia di Gaucher, tipo 1 | Malattia di Gaucher, tipo 3Cina
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National Alliance for Sickle Cell CentersBeam Therapeutics Inc.ReclutamentoTratto falciformeStati Uniti
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Nemours Children's ClinicReclutamento
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St. Louis UniversityAmerican Society for Clinical Laboratory ScienceReclutamento
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Susan CrearyNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...Completato
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Dicerna Pharmaceuticals, Inc.TerminatoIperossaluria primaria di tipo 1Olanda, Germania
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University of British ColumbiaCompletato
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); University of Texas Southwestern...TerminatoMalattie ematologiche | Anemia, anemia falciformeStati Uniti
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Medical University of South CarolinaCompletatoAnemia, anemia falciformeStati Uniti
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National Heart, Lung, and Blood Institute (NHLBI)CompletatoMalattie ematologiche | Anemia, anemia falciforme | Emoglobinopatie
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Virginia Commonwealth UniversityNational Heart, Lung, and Blood Institute (NHLBI)CompletatoAnemia, anemia falciforme | Malattia del sangue
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Indiana UniversityChildren's Hospital Medical Center, Cincinnati; Purdue UniversityReclutamento
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Children's Hospital Medical Center, CincinnatiDoris Duke Charitable FoundationReclutamentoAnemia falciforme | Anemia falciformeStati Uniti
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Boston Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)Completato
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National Heart, Lung, and Blood Institute (NHLBI)CompletatoAnemia falciformeStati Uniti
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St. Jude Children's Research HospitalCompletato
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Ashutosh LalCompletato
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HaEmek Medical Center, IsraelCompletato
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Assiut UniversitySconosciuto
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Merck Sharp & Dohme LLCCompletatoSindromi mielodisplastiche | Anemia | Leucemia Mielomonocitica Cronica | Sindromi Mielodisplastiche (MDS) | Leucemia mielomonocitica cronica (CMML) | MDS da basso a intermedio-1Stati Uniti, Francia
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University of California, San FranciscoCompletatoAnemia falciforme | Emoglobinopatie | Talassemia | Neoplasie ematologiche | Immunodeficienze | Anemia di Fanconi | Malattie non maligne | Errori genetici congeniti del metabolismoStati Uniti
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Children's Hospital Medical Center, CincinnatiReclutamentoAnemia falciforme | Bambini, SoloStati Uniti
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Baylor College of MedicineThe Methodist Hospital Research InstituteTerminatoAnemia falciforme | Talassemia | EmoglobinopatiaStati Uniti
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy,...TerminatoTrapianto di midollo osseo da donatore consanguineo per pazienti con emoglobinopatie ad alto rischioAnemia falciforme | Talassemia | EmoglobinopatiaStati Uniti
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Instituto Estadual de Hematologia Arthur de Siqueira...SconosciutoAnemia, anemia falciforme | Anemia; Falciforme, con crisiBrasile
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Brown UniversityNational Heart, Lung, and Blood Institute (NHLBI); NovartisReclutamentoAnemia falciforme | Anemia falciforme nei bambiniAngola
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Agios Pharmaceuticals, Inc.TerminatoAnemia | Anemia, emolitico | Carenza di piruvato chinasi | Anemia da deficit di piruvato chinasiStati Uniti, Regno Unito, Italia, Spagna, Olanda
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National Heart, Lung, and Blood Institute (NHLBI)CompletatoAnemia, anemia falciforme | Malattia del sangue
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National Heart, Lung, and Blood Institute (NHLBI)CompletatoAnemia, anemia falciforme | Malattia del sangue
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletatoAnemia falciforme | Falciforme-Beta0-talassemiaStati Uniti
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CSL BehringTerminatoAnemia, anemia falciformeStati Uniti
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Steven J. HardyCompletatoAnemia, anemia falciformeStati Uniti
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Prolong PharmaceuticalsCompletatoAnemia, anemia falciformeColombia, Panama, Repubblica Dominicana, Honduras
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Duke UniversityNational Institute of Nursing Research (NINR); National Institutes of Health...Completato
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The Hospital for Sick ChildrenThe Physicians' Services Incorporated FoundationCompletato
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National Heart, Lung, and Blood Institute (NHLBI)Completato
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Sohag UniversityAssiut UniversityAttivo, non reclutanteInfezione da parvovirus B19Egitto
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Children's Hospital Los AngelesNovartisNon ancora reclutamento