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Clinical Trials on 유전 질환, X-연관 in United States
총 7930 건
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University of FloridaUnited States Department of Defense완전한
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)완전한
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Boston Children's HospitalBeth Israel Deaconess Medical Center완전한
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Fairview University Medical Center종료됨면역 결핍 증후군 | 공통 변수 면역결핍 | 중증 복합 면역결핍 | 만성 육아종증 | 혈구탐식림프조직구증 | 비스코트-알드리치 증후군 | 이식편대숙주병 | X-연관 무감마글로불린혈증 | 체디악-히가시 증후군 | 바이러스 관련 혈구탐식 증후군 | 백혈구 부착 결핍 증후군 | X-연관 림프증식성 증후군 | 가족성 적식세포 림프조직구증 | X-연관 하이퍼 IgM 증후군미국
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Jirair Krikor BedoyanUltragenyx Pharmaceutical Inc모병
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Eunice Kennedy Shriver National Institute of Child...종료됨취약 X 증후군 | 조기 난소 부전 | 조기폐경 | FMR1 전열변이 | 1차 Ovairan 불충분미국
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National Institute of Allergy and Infectious Diseases...완전한
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Beacon Therapeutics모집하지 않고 적극적으로
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Lundquist Institute for Biomedical Innovation at...종료됨
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TakedaTakeda Development Center Americas, Inc.모집하지 않고 적극적으로
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Denali Therapeutics Inc.초대로 등록뮤코다당증 II미국, 캐나다, 벨기에, 체코, 네덜란드
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Rare Disease Research, LLCSarepta Therapeutics, Inc.종료됨
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National Institute of Neurological Disorders and...완전한
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Beacon Therapeutics초대로 등록
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Kevin FlaniganSarepta Therapeutics, Inc.완전한
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Kevin Flanigan모집하지 않고 적극적으로
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Megan WaldropAudentes Therapeutics모집하지 않고 적극적으로
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Sarepta Therapeutics, Inc.완전한
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)완전한
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National Human Genome Research Institute (NHGRI)완전한
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Nationwide Children's HospitalAsklepios Biopharmaceutical, Inc.완전한
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Cooperative International Neuromuscular Research...완전한
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Shire완전한
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SwanBio Therapeutics, Inc.모병
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University of California, San DiegoBioMarin Pharmaceutical빼는
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Edimer Pharmaceuticals완전한
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Children's National Research InstituteFoundation to Eradicate Duchenne모집하지 않고 적극적으로
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)완전한
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St. Jude Children's Research Hospital모병
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)완전한
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of Minnesota; Nationwide...완전한