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Kliniske studier på X-bundet cerebellar ataksi
Totalt 1811 resultater
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHFullførtRett syndromCanada, Australia, Storbritannia
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ACADIA Pharmaceuticals Inc.FullførtRett syndromForente stater
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Rett Syndrome Research TrustFullført
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National Human Genome Research Institute (NHGRI)FullførtRett syndromForente stater
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Ukjent
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Assistance Publique Hopitaux De MarseilleUkjent
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationFullført
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Sheba Medical CenterUltragenyx Pharmaceutical IncUkjent
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Central Hospital, Nancy, FranceFullført
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Hugo W. Moser Research Institute at Kennedy Krieger...Avsluttet
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Sheba Medical CenterUkjent
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Maastricht University Medical CenterFullført
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Faculdades Metropolitanas UnidasUniversity of Sao PauloFullført
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityFullførtRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkjentRett syndromForente stater
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IRCCS San RaffaeleFondazione TelethonRekrutteringKronisk granulomatøs sykdom X-bundet (X-CGD)Italia
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Parc de Salut MarHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... og andre samarbeidspartnereFullførtDowns syndrom | Fragilt X-syndromSpania
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Pitié-Salpêtrière HospitalRekrutteringLaminopatier | EmerinopatierFrankrike
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Children's Hospital of Chongqing Medical UniversityRekruttering
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University Hospital, Basel, SwitzerlandNovartisFullført
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German Center for Neurodegenerative Diseases (DZNE)McMaster University; Sorbonne UniversityRekrutteringFriedreich AtaxiaØsterrike, Tyskland, Frankrike
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Great Ormond Street Hospital for Children NHS Foundation...RekrutteringAlvorlig kombinert immunsvikt, X-kobletStorbritannia
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForente stater, Storbritannia
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForente stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbeidspartnereRekruttering
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ACADIA Pharmaceuticals Inc.FullførtRett syndromForente stater
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Edison Pharmaceuticals IncTilbaketrukket
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Anavex Life Sciences Corp.Fullført
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbeidspartnereFullført
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Neuren Pharmaceuticals Limitedrettsyndrome.orgFullført
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUkjentRett syndromDanmark, Israel
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Rigshospitalet, DenmarkFullført
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)FullførtRett syndromForente stater
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Edison Pharmaceuticals IncFullført
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Boston Children's HospitalInternational Rett Syndrome FoundationFullført
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The Cleveland ClinicAvsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationFullført
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National Taiwan University HospitalUkjent
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Maastricht University Medical CenterFullført
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineFullførtRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineFullført
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Stanford UniversityAvsluttetFragilt X-syndrom (FXS) | Idiopatisk intellektuell utviklingsforstyrrelse (IDD)Forente stater
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Indiana UniversityFullførtFragilt X-syndrom | AutismespekterforstyrrelserForente stater
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University of North Carolina, Chapel HillFullførtFragilt X-syndrom | Psykose | AutismespekterforstyrrelserForente stater
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Jazz PharmaceuticalsGW PharmaceuticalsAvsluttetRett syndrom | RTTForente stater, Canada, Italia, Spania, Storbritannia, Australia
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Ovid Therapeutics Inc.Fullført
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRekrutteringFriedreich Ataxia | Nevro-degenerativ sykdomForente stater, Canada, New Zealand, Australia, India
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University of MinnesotaFriedreich's Ataxia Research Alliance; Bob Allison Ataxia Research CenterFullførtFriedreich AtaxiaForente stater