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Søk i kliniske studier for: mucopolysaccharidoses
Totalt 226 resultater
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Inventiva PharmaFullførtMukopolysakkaridose VIStorbritannia, Frankrike, Tyskland, Portugal
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtHurler syndrom | Sanfilippo syndrom type A | Sanfilippo syndrom type BForente stater
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Ultragenyx Pharmaceutical IncFullførtMukopolysakkaridose | Sly syndrom | Mukopolysakkaridose VII | MPS VIISpania, Forente stater, Portugal
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Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalFullført
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtKrabbe sykdom | Mukopolysakkaridose type II (MPS II) | Mukopolysakkaridose type I (MPS I) | Mukopolysakkaridose type III (MPS III) | Mukopolysakkaridose type VI (MPS VI)Forente stater
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BioMarin PharmaceuticalFullførtMukopolysakkaridose IVA (Morquio A syndrom)Australia
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mukopolysakkaridose type VI | Mukopolysakkaridose Type IV | Mukopolysakkaridose type VIIForente stater, Canada
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Masonic Cancer Center, University of MinnesotaFullførtMukopolysakkaridose I | Hurler syndromForente stater
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Masonic Cancer Center, University of MinnesotaFullførtWolman sykdom | Adrenoleukodystrofi | Metakromatisk leukodystrofi | Sanfilippo syndrom | GM1 Gangliosidosis | Globoidcelleleukodystrofi | Tay Sachs sykdom | Sandhoffs sykdom | I-celle sykdomForente stater
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Ultragenyx Pharmaceutical IncFullført
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University of Texas Southwestern Medical CenterTilbaketrukketHIV-infeksjoner | Cerebral parese | Crohns sykdom | Hurler syndrom | Juvenil revmatoid artrittForente stater
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Masonic Cancer Center, University of MinnesotaFullført
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Masonic Cancer Center, University of MinnesotaAvsluttetHurler syndrom | Mukopolysakkaridose Type IH | MPS IForente stater
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ArmaGen, IncFullført
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ArmaGen, IncFullførtMukopolysakkaridose IIForente stater, Tyskland, Filippinene
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Alexion PharmaceuticalsAvsluttetMPS IIIB (Sanfilippo B-syndrom)Spania, Forente stater, Brasil, Storbritannia, Portugal, Italia
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Lundquist Institute for Biomedical Innovation at...AvsluttetMukopolysakkaridose I | Mukopolysakkaridose II | Mukopolysakkaridose VIForente stater
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Alexion PharmaceuticalsFullførtMukopolysakkaridose IIIBForente stater, Storbritannia, Spania
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Alexion PharmaceuticalsAvsluttetMukopolysakkaridose III, Type B (MPS IIIB) | Sanfilippo BStorbritannia
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Nadia Ali, PhDBioMarin PharmaceuticalFullførtMorquio A syndrom | Mukopolysakkaridose IV AForente stater
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Masonic Cancer Center, University of MinnesotaFullførtMukopolysakkaridose | Hurler syndrom | Sfingolipidoser | Peroksisomale lidelser | Krabbe sykdom | Adrenoleukodystrofi (ALD) | Hunters syndrom | Sly syndrom | Fucosidosis | Aspartylglucosaminuri | Alfa mannosidose | Metakromatisk leukodystrofi (MLD) | Maroteaux-Lamy syndromForente stater
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Children's Hospital of Eastern OntarioFullført
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Mackay Memorial HospitalBioMarin PharmaceuticalUkjent
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Masonic Cancer Center, University of MinnesotaFullførtMukopolysakkaridose I | Mukopolysakkaridose VI | Mannosidose | Mukolipidose type II (I-cellesykdom)Forente stater
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Masonic Cancer Center, University of MinnesotaAvsluttetSfingolipidoser | Niemann-Pick sykdom, type C | Krabbe sykdom | Sly syndrom | Fucosidosis | Aspartylglucosaminuri | Alfa mannosidose | Hurlers syndrom | Maroteaux-Lamy syndrom | Wolmans sykdom | Niemann-Pick sykdom type BForente stater
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University Hospital HeidelbergFullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mestringsatferd | Mukopolysakkaridose type III | AtferdsforstyrrelserTyskland
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Manchester Royal Eye HospitalBioMarin PharmaceuticalUkjentMukopolysakkaridoserStorbritannia
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GlaxoSmithKlineFullførtMukopolysakkaridose IIJapan
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Lundquist Institute for Biomedical Innovation at...FullførtMukopolysakkaridose type I | Mukopolysakkaridose type II | Mukopolysakkaridose type VIForente stater
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BioMarin PharmaceuticalFullførtMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVATaiwan, Forente stater, Italia, Storbritannia
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LYSOGENEFullførtMukopolysakkaridose type III A | Sanfilippo sykdom type AFrankrike
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Joyce FoxUltragenyx Pharmaceutical IncIkke lenger tilgjengeligMukopolysakkaridose type 7Forente stater
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Alexion PharmaceuticalsFullførtMPS IIIB (Sanfilippo Syndrome)Spania, Nederland, Storbritannia, Forente stater, Brasil
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalTilbaketrukketMukopolysakkaridose IV | Morquio A DiseaseStorbritannia
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Alexion PharmaceuticalsFullførtMPS IIIB (Sanfilippo B-syndrom)Storbritannia
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Children's Hospital Los AngelesFullførtGranulom | Anemi | Trombocytopeni | Nøytropeni | Sigdcellesykdom | Thalassemi | Niemann-Pick sykdom | Wiskott-Aldrich syndrom | Osteopetrose | Fucosidosis | Chediak Higashi syndrom | Hurler sykdomForente stater
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVAForente stater, Storbritannia, Canada, Tyskland
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Green Cross CorporationUkjentMukopolysakkaridose II
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbeidspartnereFullførtMukopolysakkaridose I | Scheie syndrom | Lysosomal lagringssykdom | Kognitiv nedgang | Hurler-Scheie syndromForente stater
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IVA | Mukopolysakkaridose IVAStorbritannia, Forente stater, Tyskland
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation og andre samarbeidspartnereFullførtMukopolysakkaridose type IIIA | Mukopolysakkaridose Type IIIBForente stater
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IV A | Mukopolysakkaridose IVAStorbritannia
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalFullførtMPS IVA | Maroteaux Lamy syndrom | MPS VI | Morquio syndrom AForente stater
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Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...FullførtMukopolysakkaridose VI | Mukopolysakkaridose IV AForente stater
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCFullførtMukopolysakkaridose I | Hurler-Scheie syndrom | Hurlers syndromForente stater, Canada, Tyskland
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCFullførtMukopolysakkaridose I | Scheie syndrom | Hurler syndrom | Hurler-Scheie syndromNederland, Frankrike, Tyskland, Storbritannia
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCFullførtMukopolysakkaridose I | Scheie syndrom | Hurlers syndrom | Hurler-Scheie syndromForente stater, Canada, Storbritannia, Brasil, Tyskland, Italia, Nederland
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCFullførtMukopolysakkaridose I | Scheie syndrom | Hurlers syndrom | Hurler-Scheie syndromBrasil, Canada
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BioMarin PharmaceuticalAvsluttetMorquio A syndrom | MPS IV A | Mukopolysakkaridose IVAFrankrike, Storbritannia, Taiwan, Forente stater, Argentina, Nederland, Canada, Brasil, Tyskland, Italia
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Emory UniversityBioMarin PharmaceuticalAvsluttetMukopolysakkaridose type IVAForente stater