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Kliniske forsøg med Cerebral folattransportmangel
I alt 220 resultater
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Kyowa Kirin Co., Ltd.Aktiv, ikke rekrutterende
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Massachusetts General HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases...RekrutteringX-bundet hypofosfatæmi | Hypofosfatæmisk rakitt | Hypophosphatemisk rakitt, X-Linked DominantForenede Stater
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Wake Forest University Health SciencesAfsluttetHypofosfatæmi | X-bundet hypofosfatæmi | Venstre ventrikulær hypertrofi | Renin-angiotensin systemetForenede Stater
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Masonic Cancer Center, University of MinnesotaAfsluttet
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Masonic Cancer Center, University of MinnesotaAfsluttet
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)AfsluttetFanconi AnæmiForenede Stater
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Afsluttet
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Fairview University Medical CenterAfsluttet
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Dana-Farber Cancer InstituteUkendtFanconis anæmiForenede Stater
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Assistance Publique - Hôpitaux de ParisEuroFancolenAfsluttet
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Masonic Cancer Center, University of MinnesotaAfsluttet
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)AfsluttetFanconi AnæmiForenede Stater
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Shenzhen Geno-Immune Medical InstituteUkendt
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Medical College of WisconsinMemorial Sloan Kettering Cancer CenterAfsluttet
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Neena Kapoor, M.D.Trukket tilbage
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National Heart, Lung, and Blood Institute (NHLBI)Afsluttet
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital...Afsluttet
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)AfsluttetFanconi AnæmiForenede Stater, Brasilien
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentAfsluttet
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University of MinnesotaUkendt
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Kyowa Kirin Korea Co., Ltd.RekrutteringFGF23-relateret hypofosfatæmisk rakitt og osteomalaciKorea, Republikken
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University of AarhusAfsluttetX-bundet hypofosfatæmi | Arvelig hypofosfatæmiDanmark
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Kyowa Kirin Pharmaceutical Development LtdAfsluttetX-forbundet hypofosfatæmiDet Forenede Kongerige
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Rambam Health Care CampusAfsluttetAstma | D-vitamin resistent rakittIsrael
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Boston Children's HospitalAfsluttet
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Masonic Cancer Center, University of MinnesotaAfsluttetFanconi AnæmiForenede Stater
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERAfsluttet
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiAfsluttet
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University...AfsluttetFANCONI AnæmiForenede Stater
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University of MinnesotaAfsluttet
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Fondation Ophtalmologique Adolphe de RothschildAfsluttetHIV seropositivitetFrankrig
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...AfsluttetFanconi Anæmi | Alvorlig aplastisk anæmiForenede Stater
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Beijing Tiantan HospitalUkendtJernmangel | Cerebralt infarkt | Demens, Vaskulær | TIA | Vaskulær kognitiv svækkelseKina
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRekrutteringMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater, Det Forenede Kongerige, Holland
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Rare Thyroid Therapeutics International ABVitaccess LtdAfsluttetAllan-Herndon-Dudley syndrom | Monocarboxylat Transporter 8 (MCT8) mangelDet Forenede Kongerige
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Rocket Pharmaceuticals Inc.UkendtFanconi Anæmi Komplementeringsgruppe AForenede Stater
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Children's Hospital Medical Center, CincinnatiAmgenAfsluttet
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Rocket Pharmaceuticals Inc.Tilmelding efter invitationFanconi Anæmi | Fanconi Anæmi Komplementeringsgruppe ASpanien
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Inozyme PharmaIkke rekrutterer endnuGeneraliseret arteriel forkalkning af spædbørn | Autosomal recessiv hypophosphatæmisk rakitt | Ectonucleotid Pyrophosphatase/phosphodiesterase1 mangel | ATP-bindende kassette Underfamilie C Medlem 6 Mangel
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Assistance Publique - Hôpitaux de ParisAfsluttetIntellektuel mangel | Cerebral abnormitetFrankrig
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Genzyme, a Sanofi CompanyGodkendt til markedsføringGlykogenopbevaringssygdom type II (GSD-II) | Sygdom med syre-maltase-mangel | Glykogenose 2 | Pompes sygdom (sen-debut)Forenede Stater
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National Center for Research Resources (NCRR)University of California, San DiegoAfsluttetFanconi syndrom | Cystinose
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxLedigMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater
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First Affiliated Hospital Xi'an Jiaotong UniversitySimcere CompanyRekruttering
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Medialis Ltd.Metabolic Support UKAfsluttetX-bundet hypofosfatæmi (XLH)Det Forenede Kongerige
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Foresee Pharmaceuticals Co., Ltd.RekrutteringFanconi AnæmiForenede Stater
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria... og andre samarbejdspartnereAfsluttetFanconi AnæmiSpanien
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Cystinosis Research FoundationUkendtCystinose | Nefropatisk cystinose | Renal Fanconi syndromForenede Stater
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereTilmelding efter invitationPrimær hyperoxaluri type 3 | Diabetes mellitus | Hæmofili A | Hæmofili B | Arvelig fruktoseintolerance | Cystisk fibrose | Faktor VII-mangel | Fenylketonuri | Seglcellesygdom | Dravet syndrom | Duchennes muskeldystrofi | Prader-Willi syndrom | Fragilt X syndrom | Kronisk granulomatøs sygdom | Rett syndrom | Wilsons sygdom | Niemann-Pick... og andre forholdForenede Stater
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Genzyme, a Sanofi CompanyAfsluttetPompes sygdom (sen debut) | Glykogenopbevaringssygdom type II (GSD-II) | Sygdom med syre-maltase-mangel | Glykogenose 2Holland