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Kliniske forsøg med Muskeldystrofi, Duchenne
I alt 50639 resultater
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Sarepta Therapeutics, Inc.Hoffmann-La RocheTilmelding efter invitation
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Mallinckrodt ARD LLCAfsluttetMuskeldystrofi, DuchenneSpanien, Bulgarien, Italien, Forenede Stater, Mexico, Israel, Serbien, Kalkun
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Sarepta Therapeutics, Inc.AfsluttetMuskeldystrofi, DuchenneForenede Stater
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Cooperative International Neuromuscular Research...Afsluttet
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Seoul National University HospitalIkke rekrutterer endnuMuskeldystrofi, Duchenne | Øvre ekstremitet | Ortotiske enhederKorea, Republikken
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Avidity Biosciences, Inc.Tilmelding efter invitationDuchennes muskeldystrofi | DMD | Exon 44 | DuchenneForenede Stater
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Santhera PharmaceuticalsAfsluttetMuskeldystrofi, Duchenne | Ambulant plejeForenede Stater, Spanien, Østrig, Belgien, Frankrig, Tyskland, Italien, Holland, Sverige, Schweiz
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of... og andre samarbejdspartnereAfsluttetKardiomyopati | Duchenne muskeldystrofi (DMD)Forenede Stater
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University Children's Hospital, ZurichUkendtDuchenne / Becker MuskeldystrofiSchweiz
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Cumberland PharmaceuticalsVanderbilt University Medical CenterRekrutteringKardiomyopati, dilateret | Duchenne muskeldystrofi kardiomyopatiForenede Stater
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Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RekrutteringLem-bælte muskeldystrofi | Neuromuskulær; Lidelse, arvelig | Duchenne/Becker muskeldystrofiForenede Stater
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Gaziosmanpasa Research and Education HospitalAfsluttetDuchenne eller Becker muskeldystrofiKalkun
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PTC TherapeuticsAfsluttetSygdomme i nervesystemet | Genetiske sygdomme, medfødte | Genetiske sygdomme, X-forbundet | Muskelsygdomme | Neuromuskulære sygdomme | Muskeldystrofier | Muskellidelser, atrofisk | Muskeldystrofi, Duchenne | Muskuloskeletal sygdomForenede Stater, Taiwan, Indien, Korea, Republikken, Thailand, Australien, Brasilien, Bulgarien, Canada, Kina, Hong Kong, Malaysia, Mexico, Polen, Puerto Rico, Den Russiske Føderation, Kalkun, Japan
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ItalfarmacoAfsluttetDuchenne og Beckers muskeldystrofi | Polycytæmi VeraCanada
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases...Ikke rekrutterer endnuMuskeldystrofi | Dyrke motion | Duchennes muskeldystrofi | Vasodilatation | DMD | Muskeldystrofi hos børn | Duchennes sygdom
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InCor Heart InstituteUniversity of Sao Paulo; Federal University of Minas GeraisAfsluttetMyokardiefibrose | Muskeldystrofier
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Hôpital CochinAssociation Monégasque contre les MyopathiesUkendtDuchennes muskeldystrofi | Duchenne muskeldystrofi-associeret dilateret kardiomyopatiFrankrig
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Capricor Inc.AfsluttetDuchennes muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...AfsluttetMuskeldystrofi, DuchenneForenede Stater
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RSPR Pharma ABAfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofiSverige
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National Institute of Neurological Disorders and...AfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...AfsluttetMuskeldystrofi, DuchenneForenede Stater
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CureDuchenneRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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The Duchenne RegistryParent Project Muscular DystrophyRekruttering
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University Hospital, MontpellierUkendtMuskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofiFrankrig
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University of North Carolina, Chapel HillNational Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbejdspartnereAfsluttetMuskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofi | Limb-Girdle muskeldystrofiForenede Stater
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Massachusetts General HospitalAfsluttetDuchennes muskeldystrofi | Dystrofinopati | Beckers muskeldystrofiForenede Stater
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Laurent ServaisSYSNAVRekrutteringDuchennes muskeldystrofi | Fascioscapulohumeral muskeldystrofiBelgien
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)AfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofi | Lembælte muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...AfsluttetMuskeldystrofi, DuchenneForenede Stater, Canada, Argentina, Australien, Israel, Italien
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Rigshospitalet, DenmarkIkke rekrutterer endnuMuskeldystrofi | Duchennes muskeldystrofi | Beckers muskeldystrofiDanmark
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Nationwide Children's HospitalParent Project Muscular DystrophyRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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University of FloridaChildren's Hospital of Philadelphia; National Institute of Arthritis and... og andre samarbejdspartnereRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofiForenede Stater
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Catholic University, ItalyUkendtDuchennes muskeldystrofi | Beckers muskeldystrofiItalien
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's... og andre samarbejdspartnereRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofi | Myotonisk dystrofi | Facioscapulohumeral muskeldystrofiForenede Stater
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ENCellIkke rekrutterer endnuDuchennes muskeldystrofiKorea, Republikken
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Ikke rekrutterer endnu
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Percheron TherapeuticsRekrutteringEn undersøgelse af ATL1102 eller placebo hos deltagere med ikke-ambulatorisk Duchenne muskeldystrofiDuchennes muskeldystrofiKalkun, Det Forenede Kongerige, Australien, Serbien, Bulgarien
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Sqy TherapeuticsBiotrialRekrutteringDuchennes muskeldystrofiFrankrig
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...Rekruttering
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REGENXBIO Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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PfizerRekrutteringDuchennes muskeldystrofiForenede Stater
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Gülsena UtkuRekruttering
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital... og andre samarbejdspartnereRekruttering
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Samsung Medical CenterRekrutteringDuchennes muskeldystrofiKorea, Republikken
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Sohag UniversityIkke rekrutterer endnuDuchennes muskeldystrofiEgypten
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Massachusetts General HospitalBoston Children's HospitalRekrutteringDuchennes muskeldystrofiForenede Stater
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University of PittsburghRekrutteringDuchennes muskeldystrofiForenede Stater
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Ning Wang, MD., PhD.Rekruttering
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CHU de Quebec-Universite LavalRekrutteringDuchennes muskeldystrofiCanada